TW202346596A - 工程化的ａｄａｒ招募ｒｎａ以及在ｕｓｈｅｒ綜合症中的使用方法 - Google Patents
工程化的ａｄａｒ招募ｒｎａ以及在ｕｓｈｅｒ綜合症中的使用方法 Download PDFInfo
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- A61K48/005—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'active' part of the composition delivered, i.e. the nucleic acid delivered
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- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
- C12N15/09—Recombinant DNA-technology
- C12N15/10—Processes for the isolation, preparation or purification of DNA or RNA
- C12N15/102—Mutagenizing nucleic acids
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- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
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- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
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- C12N15/90—Stable introduction of foreign DNA into chromosome
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12Y305/04004—Adenosine deaminase (3.5.4.4)
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12N2740/16011—Human Immunodeficiency Virus, HIV
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- C12N2740/16043—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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- C—CHEMISTRY; METALLURGY
- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
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- C12N2750/14111—Dependovirus, e.g. adenoassociated viruses
- C12N2750/14141—Use of virus, viral particle or viral elements as a vector
- C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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- Crystallography & Structural Chemistry (AREA)
- Mycology (AREA)
- Epidemiology (AREA)
- Enzymes And Modification Thereof (AREA)
- Micro-Organisms Or Cultivation Processes Thereof (AREA)
Applications Claiming Priority (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| WOPCT/CN2022/085144 | 2022-04-02 | ||
| CN2022085144 | 2022-04-02 |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| TW202346596A true TW202346596A (zh) | 2023-12-01 |
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Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
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| TW112103033A TW202346596A (zh) | 2022-04-02 | 2023-01-30 | 工程化的ａｄａｒ招募ｒｎａ以及在ｕｓｈｅｒ綜合症中的使用方法 |
Country Status (2)
| Country | Link |
|---|---|
| TW (1) | TW202346596A (fr) |
| WO (1) | WO2023185231A1 (fr) |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ES2962434T3 (es) * | 2018-10-12 | 2024-03-19 | Univ Beijing | Procedimientos y composiciones para editar ARN |
| CN113122577A (zh) * | 2019-12-30 | 2021-07-16 | 博雅辑因（北京）生物科技有限公司 | 一种治疗Usher综合征的方法和其组合物 |
| WO2022007803A1 (fr) * | 2020-07-06 | 2022-01-13 | 博雅辑因（北京）生物科技有限公司 | Procédé d'édition d'arn amélioré |
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2023
- 2023-01-28 WO PCT/CN2023/073623 patent/WO2023185231A1/fr unknown
- 2023-01-30 TW TW112103033A patent/TW202346596A/zh unknown
Also Published As
| Publication number | Publication date |
|---|---|
| WO2023185231A1 (fr) | 2023-10-05 |
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