TW202045730A - 用於治療grn相關的成年發病型神經系統退化症之重組腺相關病毒 - Google Patents

用於治療grn相關的成年發病型神經系統退化症之重組腺相關病毒 Download PDF

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TW202045730A
TW202045730A TW109105680A TW109105680A TW202045730A TW 202045730 A TW202045730 A TW 202045730A TW 109105680 A TW109105680 A TW 109105680A TW 109105680 A TW109105680 A TW 109105680A TW 202045730 A TW202045730 A TW 202045730A
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raav
aav
human
sequence
grn
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TW109105680A
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克里斯欽 亨德勒
尼羅 米勒
詹姆士M 威爾森
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賓州大學委員會
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TW109105680A 2019-02-22 2020-02-21 用於治療grn相關的成年發病型神經系統退化症之重組腺相關病毒 TW202045730A (zh)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201962809329P 2019-02-22 2019-02-22
US62/809,329 2019-02-22
US201962923812P 2019-10-21 2019-10-21
US62/923,812 2019-10-21
US202062969108P 2020-02-02 2020-02-02
US62/969,108 2020-02-02

Publications (1)

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TW202045730A true TW202045730A (zh) 2020-12-16

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TW109105680A TW202045730A (zh) 2019-02-22 2020-02-21 用於治療grn相關的成年發病型神經系統退化症之重組腺相關病毒

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US (2) US12416017B2 (https=)
EP (1) EP3927381A1 (https=)
JP (2) JP7637058B2 (https=)
KR (1) KR20210131370A (https=)
CN (1) CN113710281A (https=)
AU (1) AU2020225472A1 (https=)
BR (1) BR112021015817A2 (https=)
CA (1) CA3129672A1 (https=)
CL (1) CL2021002172A1 (https=)
CO (1) CO2021011040A2 (https=)
IL (1) IL285654A (https=)
MX (1) MX2021010134A (https=)
PE (1) PE20211819A1 (https=)
SG (1) SG11202108504YA (https=)
TW (1) TW202045730A (https=)
WO (1) WO2020172490A1 (https=)

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EP4204014A1 (en) * 2020-08-26 2023-07-05 The Trustees of The University of Pennsylvania Recombinant adeno-associated virus for treatment of grn-associated adult-onset neurodegeneration
US20240033332A1 (en) * 2020-12-17 2024-02-01 Kyoto University Agent for activating a neuron
EP4473123A4 (en) * 2022-02-01 2026-03-11 Shape Therapeutics Inc STABLE CELL LINES FOR INDUCIBLE VAAR VIRION PRODUCTION
WO2024245120A1 (en) * 2023-05-26 2024-12-05 Shanghai Vitalgen Biopharma Co., Ltd. Recombinant aav vectors for treating proteinopathies in central nervous system
WO2024263567A2 (en) * 2023-06-21 2024-12-26 Eli Lilly And Company Compounds for the delivery of granulin across the blood brain barrier
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EP3927381A1 (en) 2021-12-29
BR112021015817A2 (pt) 2021-10-13
AU2020225472A1 (en) 2021-08-26
PE20211819A1 (es) 2021-09-14
US12416017B2 (en) 2025-09-16
JP2022523766A (ja) 2022-04-26
MX2021010134A (es) 2021-09-23
CL2021002172A1 (es) 2022-02-11
CA3129672A1 (en) 2020-08-27
CN113710281A (zh) 2021-11-26
US20220136008A1 (en) 2022-05-05
IL285654A (en) 2021-09-30
CO2021011040A2 (es) 2021-09-09
JP2025081439A (ja) 2025-05-27
KR20210131370A (ko) 2021-11-02
WO2020172490A1 (en) 2020-08-27
JP7637058B2 (ja) 2025-02-27
SG11202108504YA (en) 2021-09-29
US20260049335A1 (en) 2026-02-19

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