TW202022116A - 針對α－突觸核蛋白的變體ＲＮＡｉ - Google Patents
針對α－突觸核蛋白的變體ＲＮＡｉ Download PDFInfo
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- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
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- C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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- C12N2830/00—Vector systems having a special element relevant for transcription
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- C12N2830/00—Vector systems having a special element relevant for transcription
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| EP4121538A4 (en) * | 2020-03-18 | 2024-07-31 | University Of Massachusetts | OLIGONUCLEOTIDES FOR SNCA MODULATION |
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