PL4285902T3 - Wzmocniona kwaśna α-glukozydaza do leczenia choroby Pompego - Google Patents

Wzmocniona kwaśna α-glukozydaza do leczenia choroby Pompego

Info

Publication number
PL4285902T3
PL4285902T3 PL23188938.7T PL23188938T PL4285902T3 PL 4285902 T3 PL4285902 T3 PL 4285902T3 PL 23188938 T PL23188938 T PL 23188938T PL 4285902 T3 PL4285902 T3 PL 4285902T3
Authority
PL
Poland
Prior art keywords
glucosidase
treatment
pompe disease
enhanced acid
enhanced
Prior art date
Application number
PL23188938.7T
Other languages
English (en)
Inventor
Hung V. Do
Richie Khanna
Russell GOTSCHALL
Original Assignee
Amicus Therapeutics, Inc.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Amicus Therapeutics, Inc. filed Critical Amicus Therapeutics, Inc.
Publication of PL4285902T3 publication Critical patent/PL4285902T3/pl

Links

Classifications

    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K38/00Medicinal preparations containing peptides
    • A61K38/16Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
    • A61K38/43Enzymes; Proenzymes; Derivatives thereof
    • A61K38/46Hydrolases (3)
    • A61K38/47Hydrolases (3) acting on glycosyl compounds (3.2), e.g. cellulases, lactases
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61KPREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00Medicinal preparations containing organic active ingredients
    • A61K31/33Heterocyclic compounds
    • A61K31/395Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445Non condensed piperidines, e.g. piperocaine
    • AHUMAN NECESSITIES
    • A61MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61PSPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • CCHEMISTRY; METALLURGY
    • C12BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
    • C12YENZYMES
    • C12Y302/00Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
    • C12Y302/01Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
    • C12Y302/0102Alpha-glucosidase (3.2.1.20)

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Chemical & Material Sciences (AREA)
  • General Health & Medical Sciences (AREA)
  • Veterinary Medicine (AREA)
  • Public Health (AREA)
  • Organic Chemistry (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Animal Behavior & Ethology (AREA)
  • Engineering & Computer Science (AREA)
  • Epidemiology (AREA)
  • Genetics & Genomics (AREA)
  • Gastroenterology & Hepatology (AREA)
  • Biochemistry (AREA)
  • General Engineering & Computer Science (AREA)
  • Proteomics, Peptides & Aminoacids (AREA)
  • Immunology (AREA)
  • Wood Science & Technology (AREA)
  • Zoology (AREA)
  • General Chemical & Material Sciences (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
  • Enzymes And Modification Thereof (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Medicinal Preparation (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
  • Immobilizing And Processing Of Enzymes And Microorganisms (AREA)
PL23188938.7T 2015-12-30 2016-12-29 Wzmocniona kwaśna α-glukozydaza do leczenia choroby Pompego PL4285902T3 (pl)

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201562272890P 2015-12-30 2015-12-30
US201662300479P 2016-02-26 2016-02-26
US201662315412P 2016-03-30 2016-03-30
US201662402454P 2016-09-30 2016-09-30
US201662428867P 2016-12-01 2016-12-01
US201662431791P 2016-12-08 2016-12-08

Publications (1)

Publication Number Publication Date
PL4285902T3 true PL4285902T3 (pl) 2026-04-13

Family

ID=60186557

Family Applications (3)

Application Number Title Priority Date Filing Date
PL21174249.9T PL3957320T3 (pl) 2015-12-30 2016-12-29 Wzmocniona kwaśna alfa-glukozydaza do leczenia choroby Pompego
PL23188938.7T PL4285902T3 (pl) 2015-12-30 2016-12-29 Wzmocniona kwaśna α-glukozydaza do leczenia choroby Pompego
PL16826898T PL3397273T3 (pl) 2015-12-30 2016-12-29 Wzmocniona kwaśna α-glukozydaza do leczenia choroby Pompego

Family Applications Before (1)

Application Number Title Priority Date Filing Date
PL21174249.9T PL3957320T3 (pl) 2015-12-30 2016-12-29 Wzmocniona kwaśna alfa-glukozydaza do leczenia choroby Pompego

Family Applications After (1)

Application Number Title Priority Date Filing Date
PL16826898T PL3397273T3 (pl) 2015-12-30 2016-12-29 Wzmocniona kwaśna α-glukozydaza do leczenia choroby Pompego

Country Status (16)

Country Link
EP (4) EP3397273B1 (pl)
CN (1) CN108472340A (pl)
CY (1) CY1124637T1 (pl)
DK (3) DK3957320T5 (pl)
ES (3) ES2965190T3 (pl)
FI (2) FI4285902T3 (pl)
HK (1) HK1253014A1 (pl)
HR (3) HRP20231465T1 (pl)
HU (2) HUE064049T2 (pl)
LT (3) LT3957320T (pl)
PL (3) PL3957320T3 (pl)
PT (3) PT4285902T (pl)
RS (3) RS64843B1 (pl)
SI (3) SI3957320T1 (pl)
SM (3) SMT202600054T1 (pl)
TW (3) TWI849380B (pl)

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7723296B2 (en) * 2001-01-18 2010-05-25 Genzyme Corporation Methods for introducing mannose-6-phosphate and other oligosaccharides onto glycoproteins and its application thereof
EP2857036B1 (en) 2003-01-31 2016-12-21 Mount Sinai School of Medicine of New York University Combination therapy for treating protein deficiency disorders
CA2553955C (en) * 2004-02-10 2012-08-28 Zystor Therapeutics, Inc. Acid alpha-glucosidase and fragments thereof
EP3782655A1 (en) 2005-05-17 2021-02-24 Amicus Therapeutics, Inc. A method for the treatment of pompe disease using 1-deoxynojirimycin and derivatives
EP2946785B1 (en) 2008-02-12 2018-10-24 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
AU2010254092B2 (en) * 2009-05-26 2015-11-12 Amicus Therapeutics, Inc. Utilization of pharmacological chaperones to improve manufacturing and purification of biologics
SMT202100136T1 (it) 2012-05-03 2021-05-07 Amicus Therapeutics Inc Regimi posologici per il trattamento della malattia di pompe
WO2014014938A1 (en) 2012-07-17 2014-01-23 Amicus Therapeutics, Inc. Alpha-galactosidase a and 1-deoxygalactonojirimycin co-formulation
CN114540327B (zh) * 2014-09-30 2026-03-24 阿米库斯治疗学公司 具有增强的碳水化合物的高强度酸性α-葡糖苷酶

Also Published As

Publication number Publication date
EP4706779A2 (en) 2026-03-11
PT3397273T (pt) 2021-08-09
ES2965190T3 (es) 2024-04-11
FI3957320T3 (fi) 2023-11-23
EP3397273A1 (en) 2018-11-07
DK3957320T3 (da) 2023-11-27
LT3957320T (lt) 2023-12-11
FI4285902T3 (fi) 2026-02-17
ES3063549T3 (en) 2026-04-17
TW202245831A (zh) 2022-12-01
PL3397273T3 (pl) 2021-12-06
ES2883844T3 (es) 2021-12-09
RS64843B1 (sr) 2023-12-29
SMT202600054T1 (it) 2026-03-09
RS67727B1 (sr) 2026-03-31
TW201726163A (zh) 2017-08-01
CY1124637T1 (el) 2022-07-22
DK3397273T3 (da) 2021-08-09
HUE064049T2 (hu) 2024-02-28
HRP20210894T1 (hr) 2021-07-23
SI3957320T1 (sl) 2024-01-31
SI3397273T1 (sl) 2021-11-30
SMT202300412T1 (it) 2024-01-10
EP4285902A3 (en) 2024-02-21
PT3957320T (pt) 2023-11-23
RS62212B1 (sr) 2021-09-30
PL3957320T3 (pl) 2024-02-19
SMT202100452T1 (it) 2021-09-14
DK3957320T5 (da) 2024-08-05
DK4285902T3 (da) 2026-02-16
TWI753874B (zh) 2022-02-01
HUE054733T2 (hu) 2021-09-28
SI4285902T1 (sl) 2026-04-30
EP4285902B1 (en) 2025-11-19
LT3397273T (lt) 2021-06-25
EP4285902A2 (en) 2023-12-06
HK1253014A1 (zh) 2019-06-06
EP3957320A1 (en) 2022-02-23
LT4285902T (lt) 2026-02-25
TW202506173A (zh) 2025-02-16
HRP20260120T1 (hr) 2026-03-13
EP3397273B1 (en) 2021-05-19
EP3957320B1 (en) 2023-08-23
HRP20231465T1 (hr) 2024-03-01
CN108472340A (zh) 2018-08-31
TWI849380B (zh) 2024-07-21
PT4285902T (pt) 2026-02-10

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