KR102826438B1 - 디스트로핀 유전자 내의 인식 서열에 대해 특이성을 갖는 조작된 메가뉴클레아제 - Google Patents

디스트로핀 유전자 내의 인식 서열에 대해 특이성을 갖는 조작된 메가뉴클레아제 Download PDF

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KR102826438B1
KR102826438B1 KR1020237019155A KR20237019155A KR102826438B1 KR 102826438 B1 KR102826438 B1 KR 102826438B1 KR 1020237019155 A KR1020237019155 A KR 1020237019155A KR 20237019155 A KR20237019155 A KR 20237019155A KR 102826438 B1 KR102826438 B1 KR 102826438B1
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seq
delete delete
acid sequence
dmd
nucleic acid
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개리 오웬스
자넬 레이프
제임스 제퍼슨 스미스
존 모리스
케이틀린 터너
휘트니 루이스
데렉 잔츠
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프리시젼 바이오사이언시스 인코포레이티드
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KR1020237019155A 2020-11-12 2021-11-12 디스트로핀 유전자 내의 인식 서열에 대해 특이성을 갖는 조작된 메가뉴클레아제 Active KR102826438B1 (ko)

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KR1020257020856A KR20250099412A (ko) 2020-11-12 2021-11-12 디스트로핀 유전자 내의 인식 서열에 대해 특이성을 갖는 조작된 메가뉴클레아제

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US202063113131P 2020-11-12 2020-11-12
US63/113,131 2020-11-12
US202163233664P 2021-08-16 2021-08-16
US63/233,664 2021-08-16
PCT/US2021/059146 WO2022104062A1 (en) 2020-11-12 2021-11-12 Engineered meganucleases having specificity for recognition sequences in the dystrophin gene

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KR1020257020856A Pending KR20250099412A (ko) 2020-11-12 2021-11-12 디스트로핀 유전자 내의 인식 서열에 대해 특이성을 갖는 조작된 메가뉴클레아제

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US (4) US11753630B2 (https=)
EP (1) EP4244342B1 (https=)
JP (2) JP7642809B2 (https=)
KR (2) KR102826438B1 (https=)
CN (3) CN120098962A (https=)
CA (1) CA3172481A1 (https=)
IL (2) IL317538A (https=)
MX (1) MX2023005496A (https=)
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IL302733B2 (en) 2025-05-01
CA3172481A1 (en) 2022-05-19
EP4244342A1 (en) 2023-09-20
KR20250099412A (ko) 2025-07-01
CN120098962A (zh) 2025-06-06
IL302733B1 (en) 2025-01-01
MX2023005496A (es) 2023-08-04
KR20230118841A (ko) 2023-08-14
US11753630B2 (en) 2023-09-12
IL302733A (en) 2023-07-01
EP4244342B1 (en) 2026-04-01
CN116783293A (zh) 2023-09-19
CN116783293B (zh) 2025-03-18
WO2022104062A1 (en) 2022-05-19
IL317538A (en) 2025-02-01
US20240018495A1 (en) 2024-01-18
JP2025098002A (ja) 2025-07-01
US11993793B2 (en) 2024-05-28
JP2023549357A (ja) 2023-11-24
US20240002823A1 (en) 2024-01-04
US12006522B2 (en) 2024-06-11
US20230053176A1 (en) 2023-02-16
US20250034536A1 (en) 2025-01-30
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