JPWO2023190170A5 - - Google Patents

Info

Publication number
JPWO2023190170A5
JPWO2023190170A5 JP2024512359A JP2024512359A JPWO2023190170A5 JP WO2023190170 A5 JPWO2023190170 A5 JP WO2023190170A5 JP 2024512359 A JP2024512359 A JP 2024512359A JP 2024512359 A JP2024512359 A JP 2024512359A JP WO2023190170 A5 JPWO2023190170 A5 JP WO2023190170A5
Authority
JP
Japan
Prior art keywords
bond
lipid nanoparticles
nucleic acid
group
carbon atoms
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024512359A
Other languages
English (en)
Japanese (ja)
Other versions
JPWO2023190170A1 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/JP2023/011843 external-priority patent/WO2023190170A1/ja
Publication of JPWO2023190170A1 publication Critical patent/JPWO2023190170A1/ja
Publication of JPWO2023190170A5 publication Critical patent/JPWO2023190170A5/ja
Pending legal-status Critical Current

Links

JP2024512359A 2022-03-28 2023-03-24 Pending JPWO2023190170A1 (https=)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
JP2022051913 2022-03-28
PCT/JP2023/011843 WO2023190170A1 (ja) 2022-03-28 2023-03-24 核酸内封脂質ナノ粒子の製造方法及びこれを含む医薬品組成物の製造方法、並びに、核酸を細胞内又は標的細胞内に導入する方法

Publications (2)

Publication Number Publication Date
JPWO2023190170A1 JPWO2023190170A1 (https=) 2023-10-05
JPWO2023190170A5 true JPWO2023190170A5 (https=) 2026-03-19

Family

ID=88201455

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024512359A Pending JPWO2023190170A1 (https=) 2022-03-28 2023-03-24

Country Status (7)

Country Link
US (1) US20250205168A1 (https=)
EP (1) EP4501317A4 (https=)
JP (1) JPWO2023190170A1 (https=)
KR (1) KR20240161201A (https=)
CN (1) CN119136789A (https=)
CA (1) CA3247022A1 (https=)
WO (1) WO2023190170A1 (https=)

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JPH08505312A (ja) * 1992-10-16 1996-06-11 ザックセ,アンドレアス 液状分散系を製造する方法及び装置
CA2740000C (en) * 2008-10-09 2017-12-12 Tekmira Pharmaceuticals Corporation Improved amino lipids and methods for the delivery of nucleic acids
JP2011246464A (ja) * 2010-04-28 2011-12-08 Wakamoto Pharmaceutical Co Ltd ジクロフェナクナトリウムを封入した後眼部到達用ポリマーコーティングリポソーム
WO2013073480A1 (ja) * 2011-11-18 2013-05-23 日油株式会社 細胞内動態を改善したカチオン性脂質
CN105143456A (zh) * 2013-03-15 2015-12-09 不列颠哥伦比亚大学 用于转染的脂质纳米粒子和相关方法
CN111902397B (zh) 2018-03-27 2024-04-12 日油株式会社 改进了细胞内动力学的阳离子脂质
CN118697900A (zh) * 2019-01-31 2024-09-27 摩登纳特斯有限公司 制备脂质纳米颗粒的方法
EP4035686A4 (en) * 2019-09-26 2023-11-01 NOF Corporation FREEZE DRIED COMPOSITION OF LIPID NANOPARTICLES
CA3169669A1 (en) * 2020-01-31 2021-08-05 Modernatx, Inc. Methods of preparing lipid nanoparticles
JP7746280B2 (ja) 2020-03-27 2025-09-30 ジェネレーション バイオ カンパニー 新規脂質及びそれらのナノ粒子組成物

Similar Documents

Publication Publication Date Title
CA2831392C (en) Conjugated lipomers and uses thereof
JP2023010780A (ja) 活性薬剤の送達のための分岐アルキルおよびシクロアルキルを末端とする生分解性脂質
CN114716355B (zh) 一种脂质化合物、包含其的组合物及应用
WO2022235935A2 (en) Ionizable cationic lipids for rna delivery
CA3203294A1 (en) Nanomaterials comprising carbonates
WO2021060440A1 (ja) 脂質ナノ粒子の凍結乾燥組成物
RS59380B1 (sr) Jedinjenja za ciljanje isporuke leka i pojačavanje sirnk aktivnosti
EP2882706A1 (en) Amine-containing lipidoids and uses thereof
EP4452926A1 (en) Nanomaterials comprising tetravalent lipid compounds
WO2021046260A1 (en) Asialoglycoprotein receptor mediated delivery of therapeutically active conjugates
EP4685136A1 (en) Amino lipid, and lipid nanoparticles and use thereof
WO2023121975A1 (en) Ionizable amine lipids and lipid nanoparticles
WO2023121970A1 (en) Ionizable amine and ester lipids and lipid nanoparticles
JP2021193893A (ja) 改変型piggyBacトランスポゼースのポリペプチド、それをコードするポリヌクレオチド、導入キャリア、キット、細胞のゲノムに目的配列を組込む方法及び細胞製造方法
JPWO2023190170A5 (https=)
EP4598935A2 (en) Rna constructs and uses thereof
CN120682115A (zh) 一种氨基酸骨架可电离脂质及其制备方法与应用
KR20260033596A (ko) 이온화 가능한 지질
US20230099898A1 (en) Composite rna particles
JPWO2023190166A5 (https=)
CN121127452A (zh) 可电离脂质化合物、包含其的脂质载体及应用
KR20230068047A (ko) 트레할로즈 유도체 및 신규 구조 유지 화합물을 포함하는 핵산 의약품 전달용 지질나노입자의 약학 조성물
KR102947077B1 (ko) 방향족 모이어티를 가지는 지질 화합물 및 이를 포함하는 지질 나노 입자 조성물
KR102944341B1 (ko) 핵산 전달용 신규 이온화 지질
TW202400189A (zh) 可離子化脂質