JPWO2023102490A5 - - Google Patents

Info

Publication number
JPWO2023102490A5
JPWO2023102490A5 JP2024532709A JP2024532709A JPWO2023102490A5 JP WO2023102490 A5 JPWO2023102490 A5 JP WO2023102490A5 JP 2024532709 A JP2024532709 A JP 2024532709A JP 2024532709 A JP2024532709 A JP 2024532709A JP WO2023102490 A5 JPWO2023102490 A5 JP WO2023102490A5
Authority
JP
Japan
Prior art keywords
formula
sirna molecule
represented
nucleotides
epilepsy
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024532709A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024542728A (ja
JP2024542728A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/080766 external-priority patent/WO2023102490A1/en
Publication of JP2024542728A publication Critical patent/JP2024542728A/ja
Publication of JPWO2023102490A5 publication Critical patent/JPWO2023102490A5/ja
Publication of JP2024542728A5 publication Critical patent/JP2024542728A5/ja
Pending legal-status Critical Current

Links

JP2024532709A 2021-12-01 2022-12-01 てんかんの治療のための組成物及び方法 Pending JP2024542728A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163284932P 2021-12-01 2021-12-01
US63/284,932 2021-12-01
PCT/US2022/080766 WO2023102490A1 (en) 2021-12-01 2022-12-01 Compositions and methods for treatment of epilepsies

Publications (3)

Publication Number Publication Date
JP2024542728A JP2024542728A (ja) 2024-11-15
JPWO2023102490A5 true JPWO2023102490A5 (https=) 2025-12-08
JP2024542728A5 JP2024542728A5 (https=) 2025-12-08

Family

ID=86613118

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024532709A Pending JP2024542728A (ja) 2021-12-01 2022-12-01 てんかんの治療のための組成物及び方法

Country Status (8)

Country Link
EP (1) EP4441229A1 (https=)
JP (1) JP2024542728A (https=)
KR (1) KR20240159663A (https=)
CN (1) CN118974255A (https=)
AU (1) AU2022402159A1 (https=)
CA (1) CA3241122A1 (https=)
MX (1) MX2024006709A (https=)
WO (1) WO2023102490A1 (https=)

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2019218987B2 (en) * 2018-02-12 2025-04-24 Ionis Pharmaceuticals, Inc. Modified compounds and uses thereof
US20220056455A1 (en) * 2018-12-20 2022-02-24 Praxis Precision Medicines, Inc. Compositions and methods for the treatment of kcnt1 related disorders
PE20220168A1 (es) * 2019-03-15 2022-01-28 Ionis Pharmaceuticals Inc Compuestos y metodos para reducir la expresion de kcnt1

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