JPWO2023034818A5 - - Google Patents
Info
- Publication number
- JPWO2023034818A5 JPWO2023034818A5 JP2024513759A JP2024513759A JPWO2023034818A5 JP WO2023034818 A5 JPWO2023034818 A5 JP WO2023034818A5 JP 2024513759 A JP2024513759 A JP 2024513759A JP 2024513759 A JP2024513759 A JP 2024513759A JP WO2023034818 A5 JPWO2023034818 A5 JP WO2023034818A5
- Authority
- JP
- Japan
- Prior art keywords
- compound
- peg
- pkkkrkv
- side chain
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (15)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163239671P | 2021-09-01 | 2021-09-01 | |
| US63/239,671 | 2021-09-01 | ||
| US202163244915P | 2021-09-16 | 2021-09-16 | |
| US63/244,915 | 2021-09-16 | ||
| US202163290960P | 2021-12-17 | 2021-12-17 | |
| US63/290,960 | 2021-12-17 | ||
| US202263298565P | 2022-01-11 | 2022-01-11 | |
| US63/298,565 | 2022-01-11 | ||
| US202263268577P | 2022-02-25 | 2022-02-25 | |
| US63/268,577 | 2022-02-25 | ||
| US202263337574P | 2022-05-02 | 2022-05-02 | |
| US63/337,574 | 2022-05-02 | ||
| US202263354454P | 2022-06-22 | 2022-06-22 | |
| US63/354,454 | 2022-06-22 | ||
| PCT/US2022/075693 WO2023034818A1 (en) | 2021-09-01 | 2022-08-30 | Compositions and methods for skipping exon 45 in duchenne muscular dystrophy |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024532465A JP2024532465A (ja) | 2024-09-05 |
| JP2024532465A5 JP2024532465A5 (https=) | 2025-09-05 |
| JPWO2023034818A5 true JPWO2023034818A5 (https=) | 2025-09-05 |
Family
ID=83945048
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024513759A Pending JP2024532465A (ja) | 2021-09-01 | 2022-08-30 | デュシェンヌ型筋ジストロフィーにおいてエクソン４５をスキッピングするための組成物及び方法 |
Country Status (9)
| Country | Link |
|---|---|
| US (1) | US20240417429A1 (https=) |
| EP (1) | EP4395831A1 (https=) |
| JP (1) | JP2024532465A (https=) |
| KR (1) | KR20240099149A (https=) |
| AU (1) | AU2022337260A1 (https=) |
| CA (1) | CA3230279A1 (https=) |
| IL (1) | IL311138A (https=) |
| MX (1) | MX2024002365A (https=) |
| WO (1) | WO2023034818A1 (https=) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US11168141B2 (en) | 2018-08-02 | 2021-11-09 | Dyne Therapeutics, Inc. | Muscle targeting complexes and uses thereof for treating dystrophinopathies |
| EP3829595A4 (en) | 2018-08-02 | 2022-08-24 | Dyne Therapeutics, Inc. | MUSCLE-DIRECTED COMPLEXES AND USES THEREOF IN THE TREATMENT OF DYSTROPHINOPATHIES |
| US12018087B2 (en) | 2018-08-02 | 2024-06-25 | Dyne Therapeutics, Inc. | Muscle-targeting complexes comprising an anti-transferrin receptor antibody linked to an oligonucleotide and methods of delivering oligonucleotide to a subject |
| US20220193250A1 (en) | 2018-08-02 | 2022-06-23 | Dyne Therapeutics, Inc. | Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy |
| US11771776B2 (en) | 2021-07-09 | 2023-10-03 | Dyne Therapeutics, Inc. | Muscle targeting complexes and uses thereof for treating dystrophinopathies |
| US11969475B2 (en) | 2021-07-09 | 2024-04-30 | Dyne Therapeutics, Inc. | Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy |
| WO2025038901A1 (en) * | 2023-08-17 | 2025-02-20 | Entrada Therapeutics, Inc. | Cyclic peptides for delivering therapeutics |
| WO2025072246A1 (en) * | 2023-09-26 | 2025-04-03 | Entrada Therapeutics, Inc. | Compounds and methods for skipping exon 50 in duchenne muscular dystrophy |
Family Cites Families (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3613426A1 (en) * | 2014-05-21 | 2020-02-26 | Entrada Therapeutics, Inc. | Cell penetrating peptides and methods of making and using thereof |
| US20230020092A1 (en) * | 2019-12-19 | 2023-01-19 | Entrada Therapeutics, Inc. | Compositions for delivery of antisense compounds |
| US20250243244A1 (en) * | 2021-03-31 | 2025-07-31 | Entrada Therapeutics, Inc. | Cyclic cell penetrating peptides |
-
2022
- 2022-08-30 US US18/688,096 patent/US20240417429A1/en active Pending
- 2022-08-30 AU AU2022337260A patent/AU2022337260A1/en active Pending
- 2022-08-30 IL IL311138A patent/IL311138A/en unknown
- 2022-08-30 JP JP2024513759A patent/JP2024532465A/ja active Pending
- 2022-08-30 WO PCT/US2022/075693 patent/WO2023034818A1/en not_active Ceased
- 2022-08-30 CA CA3230279A patent/CA3230279A1/en active Pending
- 2022-08-30 KR KR1020247010908A patent/KR20240099149A/ko active Pending
- 2022-08-30 MX MX2024002365A patent/MX2024002365A/es unknown
- 2022-08-30 EP EP22797583.6A patent/EP4395831A1/en active Pending
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