JPWO2022266113A5 - - Google Patents

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Publication number
JPWO2022266113A5
JPWO2022266113A5 JP2024520657A JP2024520657A JPWO2022266113A5 JP WO2022266113 A5 JPWO2022266113 A5 JP WO2022266113A5 JP 2024520657 A JP2024520657 A JP 2024520657A JP 2024520657 A JP2024520657 A JP 2024520657A JP WO2022266113 A5 JPWO2022266113 A5 JP WO2022266113A5
Authority
JP
Japan
Prior art keywords
nucleic acid
tuberine
seq
acid molecule
amino acid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024520657A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024522943A (ja
JP2024522943A5 (https=
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/033452 external-priority patent/WO2022266113A1/en
Publication of JP2024522943A publication Critical patent/JP2024522943A/ja
Publication of JPWO2022266113A5 publication Critical patent/JPWO2022266113A5/ja
Publication of JP2024522943A5 publication Critical patent/JP2024522943A5/ja
Pending legal-status Critical Current

Links

JP2024520657A 2021-06-14 2022-06-14 結節性硬化症に対する遺伝子療法 Pending JP2024522943A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163210456P 2021-06-14 2021-06-14
US63/210,456 2021-06-14
PCT/US2022/033452 WO2022266113A1 (en) 2021-06-14 2022-06-14 Gene therapy for tuberous sclerosis

Publications (3)

Publication Number Publication Date
JP2024522943A JP2024522943A (ja) 2024-06-21
JPWO2022266113A5 true JPWO2022266113A5 (https=) 2026-03-16
JP2024522943A5 JP2024522943A5 (https=) 2026-03-16

Family

ID=83080777

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024520657A Pending JP2024522943A (ja) 2021-06-14 2022-06-14 結節性硬化症に対する遺伝子療法

Country Status (7)

Country Link
US (1) US20240261439A1 (https=)
EP (1) EP4355766A1 (https=)
JP (1) JP2024522943A (https=)
CN (1) CN117715928A (https=)
BR (1) BR112023026258A2 (https=)
CA (1) CA3223219A1 (https=)
WO (1) WO2022266113A1 (https=)

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5478745A (en) 1992-12-04 1995-12-26 University Of Pittsburgh Recombinant viral vector system
US6001650A (en) 1995-08-03 1999-12-14 Avigen, Inc. High-efficiency wild-type-free AAV helper functions
US6156303A (en) 1997-06-11 2000-12-05 University Of Washington Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom
US6136597A (en) 1997-09-18 2000-10-24 The Salk Institute For Biological Studies RNA export element
WO2004058166A2 (en) 2002-12-23 2004-07-15 Vical Incorporated Codon-optimized polynucleotide-based vaccines against human cytomegalovirus infection
US7561973B1 (en) 2008-07-31 2009-07-14 Dna Twopointo, Inc. Methods for determining properties that affect an expression property value of polynucleotides in an expression system
US7561972B1 (en) 2008-06-06 2009-07-14 Dna Twopointo, Inc. Synthetic nucleic acids for expression of encoded proteins
EP3624856B1 (en) 2017-05-17 2024-04-03 The General Hospital Corporation Gene therapy for tuberous sclerosis

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