JP2024522943A5 - - Google Patents

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Publication number
JP2024522943A5
JP2024522943A5 JP2024520657A JP2024520657A JP2024522943A5 JP 2024522943 A5 JP2024522943 A5 JP 2024522943A5 JP 2024520657 A JP2024520657 A JP 2024520657A JP 2024520657 A JP2024520657 A JP 2024520657A JP 2024522943 A5 JP2024522943 A5 JP 2024522943A5
Authority
JP
Japan
Application number
JP2024520657A
Other languages
Japanese (ja)
Other versions
JPWO2022266113A5 (https=
JP2024522943A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/033452 external-priority patent/WO2022266113A1/en
Publication of JP2024522943A publication Critical patent/JP2024522943A/ja
Publication of JPWO2022266113A5 publication Critical patent/JPWO2022266113A5/ja
Publication of JP2024522943A5 publication Critical patent/JP2024522943A5/ja
Pending legal-status Critical Current

Links

JP2024520657A 2021-06-14 2022-06-14 結節性硬化症に対する遺伝子療法 Pending JP2024522943A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163210456P 2021-06-14 2021-06-14
US63/210,456 2021-06-14
PCT/US2022/033452 WO2022266113A1 (en) 2021-06-14 2022-06-14 Gene therapy for tuberous sclerosis

Publications (3)

Publication Number Publication Date
JP2024522943A JP2024522943A (ja) 2024-06-21
JPWO2022266113A5 JPWO2022266113A5 (https=) 2026-03-16
JP2024522943A5 true JP2024522943A5 (https=) 2026-03-16

Family

ID=83080777

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024520657A Pending JP2024522943A (ja) 2021-06-14 2022-06-14 結節性硬化症に対する遺伝子療法

Country Status (7)

Country Link
US (1) US20240261439A1 (https=)
EP (1) EP4355766A1 (https=)
JP (1) JP2024522943A (https=)
CN (1) CN117715928A (https=)
BR (1) BR112023026258A2 (https=)
CA (1) CA3223219A1 (https=)
WO (1) WO2022266113A1 (https=)

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US5478745A (en) 1992-12-04 1995-12-26 University Of Pittsburgh Recombinant viral vector system
US6001650A (en) 1995-08-03 1999-12-14 Avigen, Inc. High-efficiency wild-type-free AAV helper functions
US6156303A (en) 1997-06-11 2000-12-05 University Of Washington Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom
US6136597A (en) 1997-09-18 2000-10-24 The Salk Institute For Biological Studies RNA export element
WO2004058166A2 (en) 2002-12-23 2004-07-15 Vical Incorporated Codon-optimized polynucleotide-based vaccines against human cytomegalovirus infection
US7561973B1 (en) 2008-07-31 2009-07-14 Dna Twopointo, Inc. Methods for determining properties that affect an expression property value of polynucleotides in an expression system
US7561972B1 (en) 2008-06-06 2009-07-14 Dna Twopointo, Inc. Synthetic nucleic acids for expression of encoded proteins
EP3624856B1 (en) 2017-05-17 2024-04-03 The General Hospital Corporation Gene therapy for tuberous sclerosis

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