JPWO2022031708A5 - - Google Patents

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Publication number
JPWO2022031708A5
JPWO2022031708A5 JP2023507726A JP2023507726A JPWO2022031708A5 JP WO2022031708 A5 JPWO2022031708 A5 JP WO2022031708A5 JP 2023507726 A JP2023507726 A JP 2023507726A JP 2023507726 A JP2023507726 A JP 2023507726A JP WO2022031708 A5 JPWO2022031708 A5 JP WO2022031708A5
Authority
JP
Japan
Prior art keywords
cell
composition
vector
nucleic acid
raav
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023507726A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023540441A5 (https=
JP2023540441A (ja
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/044351 external-priority patent/WO2022031708A1/en
Publication of JP2023540441A publication Critical patent/JP2023540441A/ja
Publication of JP2023540441A5 publication Critical patent/JP2023540441A5/ja
Publication of JPWO2022031708A5 publication Critical patent/JPWO2022031708A5/ja
Pending legal-status Critical Current

Links

JP2023507726A 2020-08-03 2021-08-03 Parkinをコードするaavベクターおよびその使用 Pending JP2023540441A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063060353P 2020-08-03 2020-08-03
US63/060,353 2020-08-03
PCT/US2021/044351 WO2022031708A1 (en) 2020-08-03 2021-08-03 Aav vectors encoding parkin and uses thereof

Publications (3)

Publication Number Publication Date
JP2023540441A JP2023540441A (ja) 2023-09-25
JP2023540441A5 JP2023540441A5 (https=) 2024-08-09
JPWO2022031708A5 true JPWO2022031708A5 (https=) 2024-08-09

Family

ID=80118490

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023507726A Pending JP2023540441A (ja) 2020-08-03 2021-08-03 Parkinをコードするaavベクターおよびその使用

Country Status (11)

Country Link
US (1) US20230304036A1 (https=)
EP (1) EP4189097A4 (https=)
JP (1) JP2023540441A (https=)
KR (1) KR20230043181A (https=)
CN (1) CN116113701A (https=)
AU (1) AU2021322113A1 (https=)
BR (1) BR112023001788A2 (https=)
CA (1) CA3190720A1 (https=)
IL (1) IL300219A (https=)
MX (1) MX2023001565A (https=)
WO (1) WO2022031708A1 (https=)

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1504108B1 (en) * 2002-02-01 2013-04-17 Oxford Biomedica (UK) Limited Lentiviral vector
AU2013243948A1 (en) * 2012-04-02 2014-10-30 Moderna Therapeutics, Inc. Modified polynucleotides for the production of proteins associated with human disease
EP3452101A2 (en) * 2016-05-04 2019-03-13 CureVac AG Rna encoding a therapeutic protein
WO2018209126A1 (en) * 2017-05-10 2018-11-15 Rowan University Diagnostic biomarkers for detecting, subtyping, and/or assessing progression of multiple sclerosis
KR102709597B1 (ko) * 2017-10-03 2024-09-26 프리베일 테라퓨틱스, 인크. 리소좀 장애를 위한 유전자 요법
CA3096293A1 (en) * 2018-04-27 2019-10-31 Rocket Pharmaceuticals, Ltd. Gene therapy for cns degeneration

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