JPWO2021081236A5 - - Google Patents
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- Publication number
- JPWO2021081236A5 JPWO2021081236A5 JP2022523436A JP2022523436A JPWO2021081236A5 JP WO2021081236 A5 JPWO2021081236 A5 JP WO2021081236A5 JP 2022523436 A JP2022523436 A JP 2022523436A JP 2022523436 A JP2022523436 A JP 2022523436A JP WO2021081236 A5 JPWO2021081236 A5 JP WO2021081236A5
- Authority
- JP
- Japan
- Prior art keywords
- c9orf72
- nucleic acid
- vector
- pharmaceutical composition
- expression cassette
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962924351P | 2019-10-22 | 2019-10-22 | |
| US62/924,351 | 2019-10-22 | ||
| PCT/US2020/056905 WO2021081236A1 (fr) | 2019-10-22 | 2020-10-22 | Vecteurs de virus adéno-associés à triple fonction (aav) pour le traitement de maladies associées à c9orf72 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023501897A JP2023501897A (ja) | 2023-01-20 |
| JPWO2021081236A5 true JPWO2021081236A5 (fr) | 2023-10-30 |
Family
ID=75620858
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022523436A Pending JP2023501897A (ja) | 2019-10-22 | 2020-10-22 | Ｃ９ｏｒｆ７２関連疾患の治療のための三重機能アデノ随伴ウイルス（ａａｖ）ベクター |
Country Status (10)
| Country | Link |
|---|---|
| US (2) | US20210147873A1 (fr) |
| EP (1) | EP4048794A4 (fr) |
| JP (1) | JP2023501897A (fr) |
| KR (1) | KR20230019063A (fr) |
| CN (1) | CN116134134A (fr) |
| AU (1) | AU2020370291A1 (fr) |
| CA (1) | CA3158518A1 (fr) |
| IL (1) | IL292384A (fr) |
| MX (1) | MX2022004771A (fr) |
| WO (1) | WO2021081236A1 (fr) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20240017911A (ko) * | 2021-06-04 | 2024-02-08 | 알닐람 파마슈티칼스 인코포레이티드 | 인간 염색체 9 개방 해독 프레임 72(C9orf72) iRNA 제제 조성물 및 이의 사용 방법 |
| WO2023077153A1 (fr) * | 2021-11-01 | 2023-05-04 | University Of Florida Research Foundation, Incorporated | Protéines de poly-ga dans la maladie d'alzheimer |
| AR128239A1 (es) * | 2022-01-10 | 2024-04-10 | Univ Pennsylvania | Composiciones y métodos útiles para el tratamiento de trastornos mediados por c9orf72 |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN107828820B (zh) * | 2010-10-27 | 2022-06-07 | 学校法人自治医科大学 | 用于向神经系统细胞导入基因的腺相关病毒粒子 |
| US9096671B2 (en) * | 2011-06-29 | 2015-08-04 | Consejo Superior De Investigaciones Cientificas (Csic) | LRP1 as key receptor for the transfer of sterified cholesterol from very-low-density lipoproteins (VLDL) to ischaemic cardiac muscle |
| CA2846307C (fr) * | 2011-08-31 | 2020-03-10 | Hospital District Of Helsinki And Uusimaa | Procede de diagnostic d'une maladie neurodegenerative |
| US11078247B2 (en) * | 2016-05-04 | 2021-08-03 | Curevac Ag | RNA encoding a therapeutic protein |
| CN113005123A (zh) * | 2017-10-23 | 2021-06-22 | 普利维尔治疗公司 | 用于神经变性疾病的基因疗法 |
-
2020
- 2020-10-22 CN CN202080089426.2A patent/CN116134134A/zh active Pending
- 2020-10-22 KR KR1020227017065A patent/KR20230019063A/ko active Search and Examination
- 2020-10-22 JP JP2022523436A patent/JP2023501897A/ja active Pending
- 2020-10-22 AU AU2020370291A patent/AU2020370291A1/en active Pending
- 2020-10-22 US US17/077,682 patent/US20210147873A1/en not_active Abandoned
- 2020-10-22 IL IL292384A patent/IL292384A/en unknown
- 2020-10-22 CA CA3158518A patent/CA3158518A1/fr active Pending
- 2020-10-22 MX MX2022004771A patent/MX2022004771A/es unknown
- 2020-10-22 WO PCT/US2020/056905 patent/WO2021081236A1/fr unknown
- 2020-10-22 EP EP20878214.4A patent/EP4048794A4/fr active Pending
-
2023
- 2023-04-24 US US18/138,361 patent/US20240067984A1/en active Pending
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