JP7838779B2 - フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター - Google Patents

フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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JP7838779B2
JP7838779B2 JP2020518812A JP2020518812A JP7838779B2 JP 7838779 B2 JP7838779 B2 JP 7838779B2 JP 2020518812 A JP2020518812 A JP 2020518812A JP 2020518812 A JP2020518812 A JP 2020518812A JP 7838779 B2 JP7838779 B2 JP 7838779B2
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lentiviral
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テイラー ラフーゼン，
チャールズ デイビッド パウザ，
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アメリカン ジーン テクノロジーズ インターナショナル インコーポレイテッド
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JP2020518812A 2017-10-02 2018-10-02 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター Active JP7838779B2 (ja)

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JP2023101880A JP2023115125A (ja) 2017-10-02 2023-06-21 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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US201762566979P 2017-10-02 2017-10-02
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PCT/US2018/053919 WO2019070674A2 (en) 2017-10-02 2018-10-02 VECTORS COMPRISING PROMOTER AND ACTIVATOR COMBINATIONS FOR THE TREATMENT OF PHENYLCETONURIA

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JP2023101880A Pending JP2023115125A (ja) 2017-10-02 2023-06-21 フェニルケトン尿症を処置するための、プロモーターとエンハンサーの組み合わせを有するベクター

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US (1) US20200318081A1 (https=)
EP (1) EP3692157A4 (https=)
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KR (1) KR20200057766A (https=)
CN (1) CN111433368A (https=)
AU (1) AU2018345745A1 (https=)
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US20100183558A1 (en) 2008-10-17 2010-07-22 Zhennan Lai Safe lentiviral vectors for targeted delivery of multiple therapeutic molecules
EP3319631A4 (en) 2015-07-08 2019-01-09 American Gene Technologies International Inc. HIV PREMUNICATION AND IMMUNOTHERAPY
CN116064678A (zh) 2016-01-15 2023-05-05 美国基因技术国际有限公司 用于活化γ-δT细胞的方法和组合物
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