JP7576293B2 - ファーバー病を治療するための組成物及び方法 - Google Patents
ファーバー病を治療するための組成物及び方法 Download PDFInfo
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| JP2024169509A (ja) * | 2017-01-13 | 2024-12-05 | アイカーン スクール オブ メディシン アット マウント サイナイ | ファーバー病を治療するための組成物及び方法 |
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| US11597917B2 (en) * | 2017-07-06 | 2023-03-07 | The Medical College Of Wisconsin, Inc. | In vitro and in vivo enrichment strategy targeting lymphocytes derived from vector transduced HSCs for therapy of disorders |
| IL312159A (en) | 2018-02-02 | 2024-06-01 | Enzyvant Therapeutics Gmbh | Methods for treating Ferber's disease |
| EP3784695B1 (en) | 2018-04-27 | 2023-08-09 | The Medical College of Wisconsin, Inc. | Use of lentivector-transduced t-rapa cells for amelioration of lysosomal storage disorders |
| US20220088158A1 (en) * | 2019-01-23 | 2022-03-24 | Aceragen, Inc. | Method of ameliorating a pro-inflammatory immunophenotype in farber disease subjects by repeated administration of a recombinant human acid ceramidase |
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| JP2015518054A (ja) | 2012-06-01 | 2015-06-25 | アイカーン スクール オブ メディシン アット マウント サイナイ | 感染の治療および予防におけるセラミドレベル |
| JP2016520519A (ja) | 2013-03-14 | 2016-07-14 | アイカーン スクール オブ メディシン アット マウント サイナイ | 治療用酸性セラミダーゼ組成物ならびにそれを作製および使用する方法 |
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| EP3568154B1 (en) * | 2017-01-13 | 2023-07-12 | Icahn School of Medicine at Mount Sinai | Compositions and methods for treating farber disease |
| WO2019060837A1 (en) * | 2017-09-25 | 2019-03-28 | Enzyvant Farber Gmbh | PROCESS FOR PRODUCING RECOMBINANT HUMAN ACID CERAMIDASE |
| IL312159A (en) * | 2018-02-02 | 2024-06-01 | Enzyvant Therapeutics Gmbh | Methods for treating Ferber's disease |
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| Publication number | Priority date | Publication date | Assignee | Title |
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| JP2015518054A (ja) | 2012-06-01 | 2015-06-25 | アイカーン スクール オブ メディシン アット マウント サイナイ | 感染の治療および予防におけるセラミドレベル |
| JP2016520519A (ja) | 2013-03-14 | 2016-07-14 | アイカーン スクール オブ メディシン アット マウント サイナイ | 治療用酸性セラミダーゼ組成物ならびにそれを作製および使用する方法 |
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| Title |
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| Ｂｉｏｃｈｉｍｉｃａ ｅｔ Ｂｉｏｐｈｙｓｉｃａ Ａｃｔａ、２０１６、１８６２、１４５９－１４７１ |
| ＥＭＢＯ Ｍｏｌｅｃｕｌａｒ Ｍｅｄｉｃｉｎｅ、２０１３、５、８２７－８４２ |
Cited By (1)
| Publication number | Priority date | Publication date | Assignee | Title |
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| JP2024169509A (ja) * | 2017-01-13 | 2024-12-05 | アイカーン スクール オブ メディシン アット マウント サイナイ | ファーバー病を治療するための組成物及び方法 |
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| EP4295903A3 (en) | 2024-03-27 |
| EP3568154A1 (en) | 2019-11-20 |
| EP3568154B1 (en) | 2023-07-12 |
| JP2020514305A (ja) | 2020-05-21 |
| MX2019008038A (es) | 2020-02-05 |
| CA3049771A1 (en) | 2018-07-19 |
| JP2024169509A (ja) | 2024-12-05 |
| EP4295903A2 (en) | 2023-12-27 |
| JOP20190164A1 (ar) | 2019-07-02 |
| US20250170225A1 (en) | 2025-05-29 |
| US20240075113A1 (en) | 2024-03-07 |
| WO2018132667A1 (en) | 2018-07-19 |
| US20220313800A1 (en) | 2022-10-06 |
| AU2025200254A1 (en) | 2025-01-30 |
| EP3568154A4 (en) | 2020-11-18 |
| JP2023011938A (ja) | 2023-01-24 |
| US20190343936A1 (en) | 2019-11-14 |
| AU2018207564A1 (en) | 2019-08-08 |
| JOP20190164B1 (ar) | 2023-09-17 |
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