JP7254815B2 - ライソゾーム病の遺伝子治療 - Google Patents

ライソゾーム病の遺伝子治療 Download PDF

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JP7254815B2
JP7254815B2 JP2020540682A JP2020540682A JP7254815B2 JP 7254815 B2 JP7254815 B2 JP 7254815B2 JP 2020540682 A JP2020540682 A JP 2020540682A JP 2020540682 A JP2020540682 A JP 2020540682A JP 7254815 B2 JP7254815 B2 JP 7254815B2
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raav
vector
itr
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sequence
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JP2020537543A5 (cg-RX-API-DMAC7.html
JP2020537543A (ja
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アベリオビック，アーサ
ヘックマン，ローラ
ライン，エルベ
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Prevail Therapeutics Inc
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JP2020540682A 2017-10-03 2018-10-03 ライソゾーム病の遺伝子治療 Active JP7254815B2 (ja)

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JP2023052515A JP2023086740A (ja) 2017-10-03 2023-03-29 ライソゾーム病の遺伝子治療
JP2024218686A JP2025063034A (ja) 2017-10-03 2024-12-13 ライソゾーム病の遺伝子治療

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US201762567296P 2017-10-03 2017-10-03
US62/567,296 2017-10-03
PCT/US2018/054225 WO2019070893A1 (en) 2017-10-03 2018-10-03 GENE THERAPIES FOR LYSOSOMAL DISORDERS

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JP2020537543A JP2020537543A (ja) 2020-12-24
JP2020537543A5 JP2020537543A5 (cg-RX-API-DMAC7.html) 2021-11-11
JP7254815B2 true JP7254815B2 (ja) 2023-04-10

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JP2023052515A Ceased JP2023086740A (ja) 2017-10-03 2023-03-29 ライソゾーム病の遺伝子治療
JP2024218686A Withdrawn JP2025063034A (ja) 2017-10-03 2024-12-13 ライソゾーム病の遺伝子治療

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US (4) US11802294B2 (cg-RX-API-DMAC7.html)
EP (1) EP3692075A4 (cg-RX-API-DMAC7.html)
JP (3) JP7254815B2 (cg-RX-API-DMAC7.html)
KR (1) KR102693318B1 (cg-RX-API-DMAC7.html)
CN (1) CN111542549A (cg-RX-API-DMAC7.html)
AU (2) AU2018346104B2 (cg-RX-API-DMAC7.html)
BR (1) BR112020006633A2 (cg-RX-API-DMAC7.html)
CA (1) CA3078371A1 (cg-RX-API-DMAC7.html)
IL (2) IL273776B2 (cg-RX-API-DMAC7.html)
MX (2) MX2020003557A (cg-RX-API-DMAC7.html)
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JP7254815B2 (ja) 2017-10-03 2023-04-10 プリベイル セラピューティクス，インコーポレーテッド ライソゾーム病の遺伝子治療
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AU2020270984B2 (en) 2019-04-10 2025-11-20 Prevail Therapeutics, Inc. Gene therapies for lysosomal disorders
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MX2023004419A (es) * 2020-10-15 2023-07-05 Prevail Therapeutics Inc Ensayo para medir la potencia de un producto farmacológico para genoterapia.
WO2023091949A2 (en) 2021-11-17 2023-05-25 Voyager Therapeutics, Inc. Compositions and methods for the treatment of neurological disorders related to glucosylceramidase beta deficiency
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WO2024229161A1 (en) 2023-05-03 2024-11-07 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to glucosylceramidase beta 1 deficiency
WO2025038805A1 (en) 2023-08-16 2025-02-20 Voyager Therapeutics, Inc. Compositions and methods for the treatment of disorders related to glucosylceramidase beta 1 deficiency
KR20250046126A (ko) * 2023-09-22 2025-04-02 주식회사 스탠드업테라퓨티스 신규한 파킨슨 병 치료제

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