JP6317675B2 - 延長リピート病を処置するためのオリゴヌクレオチド - Google Patents

延長リピート病を処置するためのオリゴヌクレオチド Download PDF

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JP6317675B2
JP6317675B2 JP2014544959A JP2014544959A JP6317675B2 JP 6317675 B2 JP6317675 B2 JP 6317675B2 JP 2014544959 A JP2014544959 A JP 2014544959A JP 2014544959 A JP2014544959 A JP 2014544959A JP 6317675 B2 JP6317675 B2 JP 6317675B2
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antisense oligonucleotide
apn
oligonucleotides
oligonucleotide
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JP2015506669A5 (enExample
JP2015506669A (ja
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ピーター リンズリー，
ピーター リンズリー，
ブライアン ジェイムス レパート，
ブライアン ジェイムス レパート，
グンナール ジェイ． ハンソン，
グンナール ジェイ． ハンソン，
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サレプタ セラピューティクス， インコーポレイテッド
サレプタ セラピューティクス， インコーポレイテッド
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JP2014544959A 2011-11-30 2012-11-30 延長リピート病を処置するためのオリゴヌクレオチド Active JP6317675B2 (ja)

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US201161565475P 2011-11-30 2011-11-30
US61/565,475 2011-11-30
PCT/US2012/067470 WO2013082548A1 (en) 2011-11-30 2012-11-30 Oligonucleotides for treating expanded repeat diseases

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JP2015506669A JP2015506669A (ja) 2015-03-05
JP2015506669A5 JP2015506669A5 (enExample) 2016-01-28
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JP2018008762A Active JP6718474B2 (ja) 2011-11-30 2018-01-23 延長リピート病を処置するためのオリゴヌクレオチド
JP2020033113A Active JP7057385B2 (ja) 2011-11-30 2020-02-28 延長リピート病を処置するためのオリゴヌクレオチド
JP2022010846A Pending JP2022048248A (ja) 2011-11-30 2022-01-27 延長リピート病を処置するためのオリゴヌクレオチド

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JP2020033113A Active JP7057385B2 (ja) 2011-11-30 2020-02-28 延長リピート病を処置するためのオリゴヌクレオチド
JP2022010846A Pending JP2022048248A (ja) 2011-11-30 2022-01-27 延長リピート病を処置するためのオリゴヌクレオチド

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US (3) US10066228B2 (enExample)
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