JP2025513932A5 - - Google Patents

Info

Publication number
JP2025513932A5
JP2025513932A5 JP2025504030A JP2025504030A JP2025513932A5 JP 2025513932 A5 JP2025513932 A5 JP 2025513932A5 JP 2025504030 A JP2025504030 A JP 2025504030A JP 2025504030 A JP2025504030 A JP 2025504030A JP 2025513932 A5 JP2025513932 A5 JP 2025513932A5
Authority
JP
Japan
Prior art keywords
nucleic acid
antisense molecule
seq
lmna
antisense
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2025504030A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025513932A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/NL2023/050168 external-priority patent/WO2023191631A1/en
Publication of JP2025513932A publication Critical patent/JP2025513932A/ja
Publication of JP2025513932A5 publication Critical patent/JP2025513932A5/ja
Pending legal-status Critical Current

Links

JP2025504030A 2022-03-30 2023-03-30 Lmna変異キャリアのための治療における使用のためのアンチセンス核酸 Pending JP2025513932A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP22165710 2022-03-30
EP22165710.9 2022-03-30
PCT/NL2023/050168 WO2023191631A1 (en) 2022-03-30 2023-03-30 Antisense nucleic acids for use in the treatment for lmna mutation carriers

Publications (2)

Publication Number Publication Date
JP2025513932A JP2025513932A (ja) 2025-04-30
JP2025513932A5 true JP2025513932A5 (https=) 2026-04-03

Family

ID=81074125

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2025504030A Pending JP2025513932A (ja) 2022-03-30 2023-03-30 Lmna変異キャリアのための治療における使用のためのアンチセンス核酸

Country Status (9)

Country Link
US (1) US20260002152A1 (https=)
EP (1) EP4499826A1 (https=)
JP (1) JP2025513932A (https=)
KR (1) KR20250021303A (https=)
CN (1) CN119790153A (https=)
AU (1) AU2023246365A1 (https=)
CA (1) CA3246987A1 (https=)
MX (1) MX2024012034A (https=)
WO (1) WO2023191631A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025096498A1 (en) * 2023-10-30 2025-05-08 Research Institute At Nationwide Children's Hospital Compositions and methods for treating diseases or conditions associated with progerin expression

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2003070918A2 (en) 2002-02-20 2003-08-28 Ribozyme Pharmaceuticals, Incorporated Rna interference by modified short interfering nucleic acid
WO2007047913A2 (en) * 2005-10-20 2007-04-26 Isis Pharmaceuticals, Inc Compositions and methods for modulation of lmna expression
WO2020061497A1 (en) * 2018-09-20 2020-03-26 Ionis Pharmaceuticals, Inc. Compositions and methods for modulation of lmna expression

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