JP2025509566A5 - - Google Patents

Info

Publication number
JP2025509566A5
JP2025509566A5 JP2024554782A JP2024554782A JP2025509566A5 JP 2025509566 A5 JP2025509566 A5 JP 2025509566A5 JP 2024554782 A JP2024554782 A JP 2024554782A JP 2024554782 A JP2024554782 A JP 2024554782A JP 2025509566 A5 JP2025509566 A5 JP 2025509566A5
Authority
JP
Japan
Prior art keywords
concentration
optionally
approximately
pharmaceutical
formulation
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024554782A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025509566A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/015112 external-priority patent/WO2023177626A1/en
Publication of JP2025509566A publication Critical patent/JP2025509566A/ja
Publication of JP2025509566A5 publication Critical patent/JP2025509566A5/ja
Pending legal-status Critical Current

Links

JP2024554782A 2022-03-14 2023-03-13 Aav医薬製品の凍結乾燥製剤 Pending JP2025509566A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263319657P 2022-03-14 2022-03-14
US63/319,657 2022-03-14
PCT/US2023/015112 WO2023177626A1 (en) 2022-03-14 2023-03-13 Lyophilized formulations of aav drug products

Publications (2)

Publication Number Publication Date
JP2025509566A JP2025509566A (ja) 2025-04-11
JP2025509566A5 true JP2025509566A5 (https=) 2026-03-23

Family

ID=85979703

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024554782A Pending JP2025509566A (ja) 2022-03-14 2023-03-13 Aav医薬製品の凍結乾燥製剤

Country Status (11)

Country Link
US (1) US20230293724A1 (https=)
EP (1) EP4493162A1 (https=)
JP (1) JP2025509566A (https=)
KR (1) KR20250002229A (https=)
CN (1) CN119072302A (https=)
AR (1) AR128785A1 (https=)
AU (1) AU2023233503A1 (https=)
CA (1) CA3245651A1 (https=)
IL (1) IL315322A (https=)
TW (1) TW202406560A (https=)
WO (1) WO2023177626A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025076729A1 (zh) * 2023-10-11 2025-04-17 朗信启昇(苏州)生物制药有限公司 包含aav的药物组合物及其制备方法
WO2025114524A1 (en) * 2023-11-30 2025-06-05 Uniqure Biopharma B.V. Formulations for viral drug products
WO2025185606A1 (en) * 2024-03-04 2025-09-12 Nanjing Legend Biotech Co., Ltd. Composition for cryoprotection of viral vector or vlp
WO2025188316A1 (en) * 2024-03-08 2025-09-12 Jaguar Gene Therapy, Llc Aav pharmaceutical formulations and methods thereof

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
BR112021009370A2 (pt) * 2018-11-14 2021-08-17 Regenxbio Inc. método de tratamento da doença de batten cln2, composição farmacêutica e kit
SG11202107645RA (en) * 2019-01-18 2021-08-30 Voyager Therapeutics Inc Methods and systems for producing aav particles
TW202332458A (zh) * 2019-04-19 2023-08-16 美商銳進科斯生物股份有限公司 腺相關病毒載體調配物及方法
WO2021071835A1 (en) * 2019-10-07 2021-04-15 Regenxbio Inc. Adeno-associated virus vector pharmaceutical composition and methods
TW202144575A (zh) * 2020-04-03 2021-12-01 美商拜奧馬林製藥公司 使用aav及治療調配物之苯酮尿症治療

Similar Documents

Publication Publication Date Title
JP2025509566A5 (https=)
JP7630443B2 (ja) アデノ随伴ウイルスベクター製剤及び方法
JP2022529002A5 (https=)
JP2021532071A5 (https=)
CN116096431A (zh) 肽修饰的aav衣壳
CN102202688B (zh) 稳定、干燥的轮状病毒疫苗、其组合物和制备其的方法
JP2025128087A5 (https=)
JP2020505936A5 (https=)
JP2022513034A5 (https=)
JP2022523679A5 (https=)
US20230293724A1 (en) Lyophilized Formulations of AAV Drug Products
JP2025537601A (ja) 組換えアデノ随伴ウイルスベクターの薬学的組成物及びその適用
JP2023536883A5 (https=)
Bennett et al. AAV6 K531 serves a dual function in selective receptor and antibody ADK6 recognition
US20250213722A1 (en) Adeno-associated virus vectors for nucleic acid delivery to retinal ganglion cells and/or retinal pigment epithelium cells
US20220265853A1 (en) Adeno-associated virus virion for gene transfer to human liver
US20210017542A1 (en) Aav6 variants
JP2023544165A5 (https=)
US20250222135A1 (en) Adeno-associated virus vectors for nucleic acid delivery across retinal regions
CN112218880A (zh) 逃避中和的肝趋向性重组aav6载体
CN119213136A (zh) 用于将核酸递送至视网膜细胞的腺相关病毒载体
HK40111097A (zh) 无包膜病毒的药物组合物
EP4328313A1 (en) Adeno-associated virus virion for treating ornithine transcarbamylase deficiency
HK40044939A (en) Liver tropic recombinant aav6 vectors that evade neutralization
RU2025139063A (ru) Препараты аденоассоциированных вирусов