JP2025506403A5 - - Google Patents
Info
- Publication number
- JP2025506403A5 JP2025506403A5 JP2024546064A JP2024546064A JP2025506403A5 JP 2025506403 A5 JP2025506403 A5 JP 2025506403A5 JP 2024546064 A JP2024546064 A JP 2024546064A JP 2024546064 A JP2024546064 A JP 2024546064A JP 2025506403 A5 JP2025506403 A5 JP 2025506403A5
- Authority
- JP
- Japan
- Prior art keywords
- grna
- seq
- nucleic acid
- target sequence
- cas9
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202263306833P | 2022-02-04 | 2022-02-04 | |
| US63/306,833 | 2022-02-04 | ||
| PCT/US2023/012284 WO2023150272A2 (en) | 2022-02-04 | 2023-02-03 | Exon skipping to treat usher syndrome |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025506403A JP2025506403A (ja) | 2025-03-11 |
| JP2025506403A5 true JP2025506403A5 (https=) | 2026-02-12 |
Family
ID=87552793
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024546064A Pending JP2025506403A (ja) | 2022-02-04 | 2023-02-03 | アッシャー症候群を処置するためのエクソンスキッピング |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20250108129A1 (https=) |
| EP (1) | EP4472675A4 (https=) |
| JP (1) | JP2025506403A (https=) |
| CN (1) | CN119325510A (https=) |
| CA (1) | CA3250864A1 (https=) |
| WO (1) | WO2023150272A2 (https=) |
Family Cites Families (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US11028388B2 (en) * | 2014-03-05 | 2021-06-08 | Editas Medicine, Inc. | CRISPR/Cas-related methods and compositions for treating Usher syndrome and retinitis pigmentosa |
| WO2019123430A1 (en) * | 2017-12-21 | 2019-06-27 | Casebia Therapeutics Llp | Materials and methods for treatment of usher syndrome type 2a and/or non-syndromic autosomal recessive retinitis pigmentosa (arrp) |
| AU2018393050A1 (en) * | 2017-12-21 | 2020-06-18 | Bayer Healthcare Llc | Materials and methods for treatment of Usher Syndrome Type 2A |
| EP4143315A1 (en) * | 2020-04-28 | 2023-03-08 | The Broad Institute Inc. | <smallcaps/>? ? ?ush2a? ? ? ? ?targeted base editing of thegene |
-
2023
- 2023-02-03 JP JP2024546064A patent/JP2025506403A/ja active Pending
- 2023-02-03 WO PCT/US2023/012284 patent/WO2023150272A2/en not_active Ceased
- 2023-02-03 CN CN202380031655.2A patent/CN119325510A/zh active Pending
- 2023-02-03 CA CA3250864A patent/CA3250864A1/en active Pending
- 2023-02-03 EP EP23750204.2A patent/EP4472675A4/en active Pending
- 2023-02-03 US US18/833,060 patent/US20250108129A1/en active Pending
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