JP2025500335A5 - - Google Patents

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Publication number
JP2025500335A5
JP2025500335A5 JP2024537335A JP2024537335A JP2025500335A5 JP 2025500335 A5 JP2025500335 A5 JP 2025500335A5 JP 2024537335 A JP2024537335 A JP 2024537335A JP 2024537335 A JP2024537335 A JP 2024537335A JP 2025500335 A5 JP2025500335 A5 JP 2025500335A5
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JP
Japan
Application number
JP2024537335A
Other languages
Japanese (ja)
Other versions
JP2025500335A (ja
JPWO2023118087A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/EP2022/086915 external-priority patent/WO2023118087A1/en
Publication of JP2025500335A publication Critical patent/JP2025500335A/ja
Publication of JPWO2023118087A5 publication Critical patent/JPWO2023118087A5/ja
Publication of JP2025500335A5 publication Critical patent/JP2025500335A5/ja
Pending legal-status Critical Current

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JP2024537335A 2021-12-21 2022-12-20 Unc13aを標的とするアンチセンスオリゴヌクレオチド Pending JP2025500335A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP21216561 2021-12-21
EP21216561.7 2021-12-21
PCT/EP2022/086915 WO2023118087A1 (en) 2021-12-21 2022-12-20 Antisense oligonucleotides targeting unc13a

Publications (3)

Publication Number Publication Date
JP2025500335A JP2025500335A (ja) 2025-01-09
JPWO2023118087A5 JPWO2023118087A5 (https=) 2026-01-06
JP2025500335A5 true JP2025500335A5 (https=) 2026-01-06

Family

ID=79018929

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024537335A Pending JP2025500335A (ja) 2021-12-21 2022-12-20 Unc13aを標的とするアンチセンスオリゴヌクレオチド

Country Status (5)

Country Link
US (1) US20240327845A1 (https=)
EP (1) EP4453207A1 (https=)
JP (1) JP2025500335A (https=)
CN (1) CN118974254A (https=)
WO (1) WO2023118087A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
GB2603454A (en) 2020-12-09 2022-08-10 Ucl Business Ltd Novel therapeutics for the treatment of neurodegenerative disorders
CA3227115A1 (en) 2021-07-21 2023-01-26 Wen-Hsuan Chang Unc13a antisense oligonucleotides
AU2023356317A1 (en) * 2022-10-05 2025-05-15 Trace Neuroscience, Inc. Unc13a antisense oligonucleotides and uses thereof
WO2025068363A1 (en) * 2023-09-29 2025-04-03 F. Hoffmann-La Roche Ag Peptide biomarker

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2016528873A (ja) * 2012-05-16 2016-09-23 ラナ セラピューティクス インコーポレイテッド 遺伝子発現を調節するための組成物及び方法
WO2022018187A1 (en) * 2020-07-23 2022-01-27 F. Hoffmann-La Roche Ag Oligonucleotides targeting rna binding protein sites
GB2603454A (en) * 2020-12-09 2022-08-10 Ucl Business Ltd Novel therapeutics for the treatment of neurodegenerative disorders
AU2022255175A1 (en) * 2021-04-06 2023-11-23 Trace Neuroscience, Inc. Compositions and methods for treating tdp-43 proteinopathy
WO2022246251A2 (en) * 2021-05-21 2022-11-24 Ionis Pharmaceuticals, Inc. Compounds for modulating unc13a expression
CA3227115A1 (en) * 2021-07-21 2023-01-26 Wen-Hsuan Chang Unc13a antisense oligonucleotides

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