JP2024543253A5 - - Google Patents

Info

Publication number
JP2024543253A5
JP2024543253A5 JP2024527624A JP2024527624A JP2024543253A5 JP 2024543253 A5 JP2024543253 A5 JP 2024543253A5 JP 2024527624 A JP2024527624 A JP 2024527624A JP 2024527624 A JP2024527624 A JP 2024527624A JP 2024543253 A5 JP2024543253 A5 JP 2024543253A5
Authority
JP
Japan
Prior art keywords
composition according
gene therapy
polynucleotide
seq
transgene
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024527624A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024543253A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/079756 external-priority patent/WO2023086966A1/en
Publication of JP2024543253A publication Critical patent/JP2024543253A/ja
Publication of JP2024543253A5 publication Critical patent/JP2024543253A5/ja
Pending legal-status Critical Current

Links

JP2024527624A 2021-11-12 2022-11-11 Ｓｌｃ６ａ１遺伝子治療のための材料及び方法 Pending JP2024543253A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163278905P 2021-11-12 2021-11-12
US63/278,905 2021-11-12
PCT/US2022/079756 WO2023086966A1 (en) 2021-11-12 2022-11-11 Materials and methods for slc6a1 gene therapy

Publications (2)

Publication Number Publication Date
JP2024543253A JP2024543253A (ja) 2024-11-20
JP2024543253A5 true JP2024543253A5 (cg-RX-API-DMAC7.html) 2025-10-27

Family

ID=86336739

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024527624A Pending JP2024543253A (ja) 2021-11-12 2022-11-11 Ｓｌｃ６ａ１遺伝子治療のための材料及び方法

Country Status (6)

Country Link
US (1) US20250002939A1 (cg-RX-API-DMAC7.html)
EP (1) EP4429715A4 (cg-RX-API-DMAC7.html)
JP (1) JP2024543253A (cg-RX-API-DMAC7.html)
AU (1) AU2022386664A1 (cg-RX-API-DMAC7.html)
CA (1) CA3238030A1 (cg-RX-API-DMAC7.html)
WO (1) WO2023086966A1 (cg-RX-API-DMAC7.html)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2024305531A1 (en) * 2023-06-13 2026-01-22 Research Institute At Nationwide Children's Hospital Materials and methods for the treatment of neurofibromin 1 mutations and diseases resulting therefrom
WO2025228976A1 (en) * 2024-04-29 2025-11-06 UCB Biopharma SRL Gene therapy

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7820380B2 (en) * 2004-05-07 2010-10-26 Celera Corporation Genetic polymorphisms associated with liver fibrosis
US12077772B2 (en) * 2019-11-08 2024-09-03 The Board Of Regents Of The University Of Texas System Transgene cassettes, AAV vectors and AAV viral vectors for the expression of human codon-optimized SLC6A1

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