JP2024521897A5 - - Google Patents

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Publication number
JP2024521897A5
JP2024521897A5 JP2023574349A JP2023574349A JP2024521897A5 JP 2024521897 A5 JP2024521897 A5 JP 2024521897A5 JP 2023574349 A JP2023574349 A JP 2023574349A JP 2023574349 A JP2023574349 A JP 2023574349A JP 2024521897 A5 JP2024521897 A5 JP 2024521897A5
Authority
JP
Japan
Prior art keywords
item
formula
ribonucleoside
items
represented
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023574349A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024521897A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/032014 external-priority patent/WO2022256565A2/en
Publication of JP2024521897A publication Critical patent/JP2024521897A/ja
Publication of JP2024521897A5 publication Critical patent/JP2024521897A5/ja
Pending legal-status Critical Current

Links

JP2023574349A 2021-06-02 2022-06-02 治療用オリゴヌクレオチドを中枢神経系に送達するための組成物及び方法 Pending JP2024521897A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163195993P 2021-06-02 2021-06-02
US63/195,993 2021-06-02
PCT/US2022/032014 WO2022256565A2 (en) 2021-06-02 2022-06-02 Compositions and methods for delivering therapeutic oligonucleotides to the central nervous system

Publications (2)

Publication Number Publication Date
JP2024521897A JP2024521897A (ja) 2024-06-04
JP2024521897A5 true JP2024521897A5 (enExample) 2025-05-28

Family

ID=84324589

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023574349A Pending JP2024521897A (ja) 2021-06-02 2022-06-02 治療用オリゴヌクレオチドを中枢神経系に送達するための組成物及び方法

Country Status (9)

Country Link
US (1) US20240287526A1 (enExample)
EP (1) EP4346845A2 (enExample)
JP (1) JP2024521897A (enExample)
KR (1) KR20240038930A (enExample)
CN (1) CN117795069A (enExample)
AU (1) AU2022286420A1 (enExample)
CA (1) CA3222212A1 (enExample)
IL (1) IL308994A (enExample)
WO (1) WO2022256565A2 (enExample)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
AU2023354001A1 (en) * 2022-09-28 2025-04-17 Atalanta Therapeutics, Inc. Compositions and methods for treatment of huntington's disease
WO2024169770A1 (zh) * 2023-02-17 2024-08-22 苏州时安生物技术有限公司 一种抑制SCN9A基因表达的siRNA、其药物组合物及用途
WO2024197280A1 (en) * 2023-03-23 2024-09-26 Atalanta Therapeutics, Inc. Compositions and methods for improved gene silencing
WO2025111497A1 (en) * 2023-11-21 2025-05-30 Ionis Pharmaceuticals, Inc. Compounds and methods for modulating acute activation
WO2025193786A1 (en) * 2024-03-12 2025-09-18 University Of Massachusetts Oligonucleotides for prnp modulation

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP3107549B1 (en) * 2014-02-20 2020-07-01 B.G. Negev Technologies and Applications Ltd. Anionic polyplexes for use in the delivery of nucleic acids
WO2019122279A1 (en) * 2017-12-22 2019-06-27 Roche Innovation Center Copenhagen A/S Oligonucleotides comprising a phosphorodithioate internucleoside linkage

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