JP2024521679A5 - - Google Patents
Info
- Publication number
- JP2024521679A5 JP2024521679A5 JP2023571569A JP2023571569A JP2024521679A5 JP 2024521679 A5 JP2024521679 A5 JP 2024521679A5 JP 2023571569 A JP2023571569 A JP 2023571569A JP 2023571569 A JP2023571569 A JP 2023571569A JP 2024521679 A5 JP2024521679 A5 JP 2024521679A5
- Authority
- JP
- Japan
- Prior art keywords
- cells
- nucleic acid
- gsh
- promoter
- cell
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163190996P | 2021-05-20 | 2021-05-20 | |
| US63/190,996 | 2021-05-20 | ||
| PCT/US2022/030024 WO2022246063A1 (en) | 2021-05-20 | 2022-05-19 | Genomic safe harbors |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024521679A JP2024521679A (ja) | 2024-06-04 |
| JP2024521679A5 true JP2024521679A5 (enExample) | 2025-05-26 |
Family
ID=84141733
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023571569A Pending JP2024521679A (ja) | 2021-05-20 | 2022-05-19 | ゲノムセーフハーバー |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20250087304A1 (enExample) |
| EP (1) | EP4352519A4 (enExample) |
| JP (1) | JP2024521679A (enExample) |
| KR (1) | KR20240023030A (enExample) |
| AU (1) | AU2022277688A1 (enExample) |
| CA (1) | CA3219160A1 (enExample) |
| WO (1) | WO2022246063A1 (enExample) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2024218715A1 (en) | 2023-04-19 | 2024-10-24 | Btl Healthcare Technologies A.S. | Culture media based on protein hydrolysate and a process for preparing thereof |
| CN121729252A (zh) * | 2023-08-31 | 2026-03-24 | 基奈治疗股份有限公司 | 用于工程化的da神经元细胞的方法和组合物 |
| US12668774B2 (en) | 2023-10-12 | 2026-06-30 | Btl Healthcare Technologies A.S. | Product, system and method of cell cultivation |
| CN118256559B (zh) * | 2024-01-24 | 2024-09-17 | 中国医学科学院阜外医院 | 制备射血分数保留的心衰的动物模型的方法 |
| WO2026064739A1 (en) * | 2024-09-23 | 2026-03-26 | Carbon Biosciences, Inc. | Parvovirus compositions and related methods for gene therapy |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2539445B1 (en) * | 2010-02-26 | 2018-03-21 | Cellectis | Use of endonucleases for inserting transgenes into safe harbor loci |
| KR102712142B1 (ko) * | 2017-07-31 | 2024-10-07 | 리제너론 파마슈티칼스 인코포레이티드 | Cas-형질전환 마우스 배아 줄기 세포 및 마우스 및 이것의 용도 |
| JP2021505159A (ja) * | 2017-12-06 | 2021-02-18 | ジェネレーション バイオ カンパニー | 修飾型閉端ｄｎａ（ｃｅｄｎａ）を使用する遺伝子編集 |
| CA3092832A1 (en) * | 2018-03-02 | 2019-09-06 | Generation Bio Co. | Identifying and characterizing genomic safe harbors (gsh) in humans and murine genomes, and viral and non-viral vector compositions for targeted integration at an identified gsh loci |
| CA3092459A1 (en) * | 2018-03-02 | 2019-09-06 | Generation Bio Co. | Closed-ended dna (cedna) vectors for insertion of transgenes at genomic safe harbors (gsh) in humans and murine genomes |
| US20200370067A1 (en) * | 2019-05-21 | 2020-11-26 | University Of Washington | Method to identify and validate genomic safe harbor sites for targeted genome engineering |
| EP4032092A4 (en) * | 2019-09-17 | 2023-12-06 | Memorial Sloan Kettering Cancer Center | Genomic safe harbors for transgene integration |
| AU2020349512A1 (en) * | 2019-09-17 | 2022-04-14 | Memorial Sloan-Kettering Cancer Center | Methods for identifying genomic safe harbors |
| CN115175987A (zh) * | 2019-09-23 | 2022-10-11 | 明尼苏达大学董事会 | 基因编辑的免疫细胞和治疗方法 |
| EP4045539A4 (en) * | 2019-10-17 | 2024-03-13 | Fate Therapeutics, Inc. | Enhanced chimeric antigen receptor for immune effector cell engineering and use thereof |
-
2022
- 2022-05-19 CA CA3219160A patent/CA3219160A1/en active Pending
- 2022-05-19 EP EP22805477.1A patent/EP4352519A4/en active Pending
- 2022-05-19 KR KR1020237041814A patent/KR20240023030A/ko active Pending
- 2022-05-19 AU AU2022277688A patent/AU2022277688A1/en active Pending
- 2022-05-19 JP JP2023571569A patent/JP2024521679A/ja active Pending
- 2022-05-19 US US18/562,737 patent/US20250087304A1/en active Pending
- 2022-05-19 WO PCT/US2022/030024 patent/WO2022246063A1/en not_active Ceased
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