JP2024521679A5 - - Google Patents
Info
- Publication number
- JP2024521679A5 JP2024521679A5 JP2023571569A JP2023571569A JP2024521679A5 JP 2024521679 A5 JP2024521679 A5 JP 2024521679A5 JP 2023571569 A JP2023571569 A JP 2023571569A JP 2023571569 A JP2023571569 A JP 2023571569A JP 2024521679 A5 JP2024521679 A5 JP 2024521679A5
- Authority
- JP
- Japan
- Prior art keywords
- cells
- nucleic acid
- gsh
- promoter
- cell
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163190996P | 2021-05-20 | 2021-05-20 | |
| US63/190,996 | 2021-05-20 | ||
| PCT/US2022/030024 WO2022246063A1 (en) | 2021-05-20 | 2022-05-19 | Genomic safe harbors |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024521679A JP2024521679A (ja) | 2024-06-04 |
| JP2024521679A5 true JP2024521679A5 (OSRAM) | 2025-05-26 |
Family
ID=84141733
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023571569A Pending JP2024521679A (ja) | 2021-05-20 | 2022-05-19 | ゲノムセーフハーバー |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20250087304A1 (OSRAM) |
| EP (1) | EP4352519A4 (OSRAM) |
| JP (1) | JP2024521679A (OSRAM) |
| KR (1) | KR20240023030A (OSRAM) |
| AU (1) | AU2022277688A1 (OSRAM) |
| CA (1) | CA3219160A1 (OSRAM) |
| WO (1) | WO2022246063A1 (OSRAM) |
Families Citing this family (3)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2024334482C1 (en) * | 2023-08-31 | 2026-04-23 | Kenai Therapeutics Inc. | Methods and compositions for engineered da neuronal cells |
| CN118256559B (zh) * | 2024-01-24 | 2024-09-17 | 中国医学科学院阜外医院 | 制备射血分数保留的心衰的动物模型的方法 |
| WO2026064739A1 (en) * | 2024-09-23 | 2026-03-26 | Carbon Biosciences, Inc. | Parvovirus compositions and related methods for gene therapy |
Family Cites Families (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2539445B1 (en) * | 2010-02-26 | 2018-03-21 | Cellectis | Use of endonucleases for inserting transgenes into safe harbor loci |
| CN110891420B (zh) * | 2017-07-31 | 2022-06-03 | 瑞泽恩制药公司 | Cas转基因小鼠胚胎干细胞和小鼠及其应用 |
| KR20200093635A (ko) * | 2017-12-06 | 2020-08-05 | 제너레이션 바이오 컴퍼니 | 변형된 폐쇄된 말단 dna (cedna)를 사용한 유전자 편집 |
| EP3759226A4 (en) * | 2018-03-02 | 2022-06-15 | Generation Bio Co. | IDENTIFICATION AND CHARACTERIZATION OF GENOMIC SAFE HARBOR (GSH) IN HUMAN AND MURINE GENOMES AND VIRAL AND NON-VIRAL VECTOR COMPOSITIONS FOR TARGETED INTEGRATION AT IDENTIFIED GSH LOCI |
| WO2019169233A1 (en) * | 2018-03-02 | 2019-09-06 | Generation Bio Co. | Closed-ended dna (cedna) vectors for insertion of transgenes at genomic safe harbors (gsh) in humans and murine genomes |
| US20200370067A1 (en) * | 2019-05-21 | 2020-11-26 | University Of Washington | Method to identify and validate genomic safe harbor sites for targeted genome engineering |
| AU2020348776A1 (en) * | 2019-09-17 | 2022-05-05 | Memorial Sloan-Kettering Cancer Center | Genomic safe harbors for transgene integration |
| WO2021055592A1 (en) * | 2019-09-17 | 2021-03-25 | Memorial Sloan-Kettering Cancer Center | Methods for identifying genomic safe harbors |
| EP4034640A4 (en) * | 2019-09-23 | 2023-10-25 | Regents Of The University Of Minnesota | GENETICALLY EDITED IMMUNE CELLS AND THERAPY METHODS |
| JP7664913B2 (ja) * | 2019-10-17 | 2025-04-18 | フェイト セラピューティクス，インコーポレイテッド | 免疫のための増強されたキメラ抗原受容体エフェクター細胞操作およびその使用 |
-
2022
- 2022-05-19 AU AU2022277688A patent/AU2022277688A1/en active Pending
- 2022-05-19 JP JP2023571569A patent/JP2024521679A/ja active Pending
- 2022-05-19 EP EP22805477.1A patent/EP4352519A4/en active Pending
- 2022-05-19 WO PCT/US2022/030024 patent/WO2022246063A1/en not_active Ceased
- 2022-05-19 KR KR1020237041814A patent/KR20240023030A/ko active Pending
- 2022-05-19 CA CA3219160A patent/CA3219160A1/en active Pending
- 2022-05-19 US US18/562,737 patent/US20250087304A1/en active Pending
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