JP2024516655A5 - - Google Patents

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Publication number
JP2024516655A5
JP2024516655A5 JP2023565998A JP2023565998A JP2024516655A5 JP 2024516655 A5 JP2024516655 A5 JP 2024516655A5 JP 2023565998 A JP2023565998 A JP 2023565998A JP 2023565998 A JP2023565998 A JP 2023565998A JP 2024516655 A5 JP2024516655 A5 JP 2024516655A5
Authority
JP
Japan
Prior art keywords
lentiviral vector
sequence
rheam
agxt
vector according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023565998A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024516655A (ja
Filing date
Publication date
Priority claimed from EP21382363.6A external-priority patent/EP4083217A1/en
Application filed filed Critical
Publication of JP2024516655A publication Critical patent/JP2024516655A/ja
Publication of JP2024516655A5 publication Critical patent/JP2024516655A5/ja
Pending legal-status Critical Current

Links

JP2023565998A 2021-04-26 2022-04-26 原発性高シュウ酸尿症1型の治療のためのin vivoレンチウイルス遺伝子療法 Pending JP2024516655A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP21382363.6 2021-04-26
EP21382363.6A EP4083217A1 (en) 2021-04-26 2021-04-26 In vivo lentiviral gene therapy for the treatment of primary hyperoxaluria type 1
PCT/EP2022/061107 WO2022229223A1 (en) 2021-04-26 2022-04-26 In vivo lentiviral gene therapy for the treatment of primary hyperoxaluria type 1

Publications (2)

Publication Number Publication Date
JP2024516655A JP2024516655A (ja) 2024-04-16
JP2024516655A5 true JP2024516655A5 (enExample) 2025-05-09

Family

ID=75746556

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023565998A Pending JP2024516655A (ja) 2021-04-26 2022-04-26 原発性高シュウ酸尿症1型の治療のためのin vivoレンチウイルス遺伝子療法

Country Status (8)

Country Link
EP (2) EP4083217A1 (enExample)
JP (1) JP2024516655A (enExample)
KR (1) KR20240004627A (enExample)
CN (1) CN117561336A (enExample)
AU (1) AU2022266057A1 (enExample)
CA (1) CA3218031A1 (enExample)
MX (1) MX2023012684A (enExample)
WO (1) WO2022229223A1 (enExample)

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP2384200B1 (en) * 2009-01-30 2013-07-10 UniQure IP B.V. Alanine-glyoxylate aminotransferase therapeutics
WO2015059701A1 (en) * 2013-10-24 2015-04-30 Medgenics Medical Israel Ltd. Micro-organs providing sustained delivery of a therapeutic polypeptide and methods of use thereof
US11008561B2 (en) * 2014-06-30 2021-05-18 Bioverativ Therapeutics Inc. Optimized factor IX gene
US11976293B2 (en) * 2016-12-05 2024-05-07 The Regents Of The University Of California Optimized lentiviral vector for stem cell gene therapy of hemoglobinopathies
US20210038744A1 (en) * 2018-02-01 2021-02-11 Bioverativ Therapeutics Inc. Use of lentiviral vectors expressing factor viii

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