JP2024501284A5 - - Google Patents

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Publication number
JP2024501284A5
JP2024501284A5 JP2023538718A JP2023538718A JP2024501284A5 JP 2024501284 A5 JP2024501284 A5 JP 2024501284A5 JP 2023538718 A JP2023538718 A JP 2023538718A JP 2023538718 A JP2023538718 A JP 2023538718A JP 2024501284 A5 JP2024501284 A5 JP 2024501284A5
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JP
Japan
Prior art keywords
promoter
composition according
nonviral
phagocytic
inhibitor
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023538718A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024501284A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/073084 external-priority patent/WO2022140788A1/en
Publication of JP2024501284A publication Critical patent/JP2024501284A/ja
Publication of JP2024501284A5 publication Critical patent/JP2024501284A5/ja
Pending legal-status Critical Current

Links

JP2023538718A 2020-12-23 2021-12-22 非ウイルス遺伝子治療を強化する方法 Pending JP2024501284A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063130105P 2020-12-23 2020-12-23
US63/130,105 2020-12-23
PCT/US2021/073084 WO2022140788A1 (en) 2020-12-23 2021-12-22 Methods of enhancing non-viral gene therapy

Publications (2)

Publication Number Publication Date
JP2024501284A JP2024501284A (ja) 2024-01-11
JP2024501284A5 true JP2024501284A5 (https=) 2024-12-20

Family

ID=82158434

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023538718A Pending JP2024501284A (ja) 2020-12-23 2021-12-22 非ウイルス遺伝子治療を強化する方法

Country Status (8)

Country Link
US (1) US20240074986A1 (https=)
EP (1) EP4267253A4 (https=)
JP (1) JP2024501284A (https=)
CN (1) CN116964207A (https=)
AU (1) AU2021410086A1 (https=)
CA (1) CA3206000A1 (https=)
MX (1) MX2023007609A (https=)
WO (1) WO2022140788A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2023122062A1 (en) * 2021-12-21 2023-06-29 Cornell University Methods for enhanced nucleic acid delivery
WO2024054901A1 (en) * 2022-09-09 2024-03-14 Spark Therapeutics, Inc. Piperazine compounds
EP4583861A1 (en) * 2022-09-09 2025-07-16 Spark Therapeutics, Inc. Enhancing non-viral dna delivery and expression
WO2025096940A1 (en) * 2023-11-01 2025-05-08 Spark Therapeutics, Inc. Lipid compounds

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20140141065A1 (en) * 2012-11-19 2014-05-22 Discovery Genomics, Inc. Method to achieve extended expression of dna infused into liver
WO2019018640A1 (en) * 2017-07-21 2019-01-24 Novartis Ag POSOLOGICAL REGIMES FOR ANTI-GITREN ANTIBODIES AND USES THEREOF
WO2019226650A1 (en) * 2018-05-23 2019-11-28 Modernatx, Inc. Delivery of dna
EP3934700A4 (en) * 2019-03-06 2022-12-14 Generation Bio Co. NON-ACTIVE LIPID NANOPARTICLES WITH CAPSID-FREE, NON-VIRAL DNA

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