JP2024084849A5 - - Google Patents
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- JP2024084849A5 JP2024084849A5 JP2024063151A JP2024063151A JP2024084849A5 JP 2024084849 A5 JP2024084849 A5 JP 2024084849A5 JP 2024063151 A JP2024063151 A JP 2024063151A JP 2024063151 A JP2024063151 A JP 2024063151A JP 2024084849 A5 JP2024084849 A5 JP 2024084849A5
- Authority
- JP
- Japan
- Prior art keywords
- cells
- nucleic acid
- ucoe
- seq
- nucleotide sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
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Applications Claiming Priority (4)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201762488523P | 2017-04-21 | 2017-04-21 | |
| US62/488,523 | 2017-04-21 | ||
| JP2019557373A JP7471821B2 (ja) | 2017-04-21 | 2018-04-19 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
| PCT/US2018/028331 WO2018195297A1 (en) | 2017-04-21 | 2018-04-19 | Optimized lentiviral vector for xla gene therapy |
Related Parent Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019557373A Division JP7471821B2 (ja) | 2017-04-21 | 2018-04-19 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2024084849A JP2024084849A (ja) | 2024-06-25 |
| JP2024084849A5 true JP2024084849A5 (enExample) | 2024-10-17 |
| JP7696039B2 JP7696039B2 (ja) | 2025-06-19 |
Family
ID=63856377
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019557373A Active JP7471821B2 (ja) | 2017-04-21 | 2018-04-19 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
| JP2024063151A Active JP7696039B2 (ja) | 2017-04-21 | 2024-04-10 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Family Applications Before (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019557373A Active JP7471821B2 (ja) | 2017-04-21 | 2018-04-19 | Ｘｌａ遺伝子療法用の最適化されたレンチウイルスベクター |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20200325458A1 (enExample) |
| EP (1) | EP3612238A4 (enExample) |
| JP (2) | JP7471821B2 (enExample) |
| CN (1) | CN110809627A (enExample) |
| AU (1) | AU2018256412B2 (enExample) |
| WO (1) | WO2018195297A1 (enExample) |
Families Citing this family (4)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP3801640A4 (en) | 2018-05-30 | 2022-03-23 | The Regents Of The University Of California | GENE EDIT OF MONOGENIC DISEASES IN HUMAN HEMATOPOIETIC STEM CELLS - CORRECTION OF X-LINKED AGAMMAGLOBULINEMIA (XLA) |
| KR20210049133A (ko) | 2018-08-24 | 2021-05-04 | 씨에스엘 베링 진 테라피, 인크. | 무혈청 배지에서 벡터 제조 |
| US11464872B2 (en) * | 2020-12-07 | 2022-10-11 | Noga Therapeutics Ltd. | Lentiviral vectors for therapeutic expression of BTK in haematopoietic cells |
| WO2025215591A1 (en) | 2024-04-12 | 2025-10-16 | Csl Behring L.L.C. | Modified vectors for xla gene therapy |
Family Cites Families (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6974667B2 (en) * | 2000-06-14 | 2005-12-13 | Gene Logic, Inc. | Gene expression profiles in liver cancer |
| US20160004814A1 (en) * | 2012-09-05 | 2016-01-07 | University Of Washington Through Its Center For Commercialization | Methods and compositions related to regulation of nucleic acids |
-
2018
- 2018-04-19 AU AU2018256412A patent/AU2018256412B2/en active Active
- 2018-04-19 WO PCT/US2018/028331 patent/WO2018195297A1/en not_active Ceased
- 2018-04-19 JP JP2019557373A patent/JP7471821B2/ja active Active
- 2018-04-19 CN CN201880043435.0A patent/CN110809627A/zh active Pending
- 2018-04-19 EP EP18788504.1A patent/EP3612238A4/en active Pending
- 2018-04-19 US US16/605,740 patent/US20200325458A1/en active Pending
-
2024
- 2024-04-10 JP JP2024063151A patent/JP7696039B2/ja active Active
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