JP2023548478A - 細胞のゲノム改変用組成物及び方法ならびにその使用 - Google Patents

細胞のゲノム改変用組成物及び方法ならびにその使用 Download PDF

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JP2023548478A
JP2023548478A JP2023526200A JP2023526200A JP2023548478A JP 2023548478 A JP2023548478 A JP 2023548478A JP 2023526200 A JP2023526200 A JP 2023526200A JP 2023526200 A JP2023526200 A JP 2023526200A JP 2023548478 A JP2023548478 A JP 2023548478A
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cell
endogenous gene
sequence
cells
transgene
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アーロン クーパー
アンジェラ ボローズ
ペイ-ケン スー
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アーセナル バイオサイエンシズ インコーポレイテッド
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    • C12N9/14Hydrolases (3)
    • C12N9/16Hydrolases (3) acting on ester bonds (3.1)
    • C12N9/22Ribonucleases [RNase]; Deoxyribonucleases [DNase]

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JP2023526200A 2020-10-29 2021-10-29 細胞のゲノム改変用組成物及び方法ならびにその使用 Pending JP2023548478A (ja)

Applications Claiming Priority (3)

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US202063107401P 2020-10-29 2020-10-29
US63/107,401 2020-10-29
PCT/US2021/057457 WO2022094348A1 (en) 2020-10-29 2021-10-29 Compositions and methods of genomic modification of cells and uses thereof

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JP2023548478A true JP2023548478A (ja) 2023-11-17
JP2023548478A5 JP2023548478A5 (https=) 2024-11-05
JPWO2022094348A5 JPWO2022094348A5 (https=) 2024-11-05

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US (1) US20230365997A1 (https=)
EP (1) EP4236969A4 (https=)
JP (1) JP2023548478A (https=)
CN (1) CN116490606A (https=)
WO (1) WO2022094348A1 (https=)

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CN116784280B (zh) * 2023-08-10 2025-08-19 广东药康生物科技有限公司 一种tfrc人源化小鼠模型的构建方法及其应用

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KR20210020873A (ko) * 2018-04-05 2021-02-24 주노 쎄러퓨티크스 인코퍼레이티드 재조합 수용체를 발현하는 τ 세포, 관련 폴리뉴클레오티드 및 방법
CN113840920A (zh) * 2019-03-14 2021-12-24 加利福尼亚大学董事会 合并的敲入筛选和在内源基因座控制下共表达的异源多肽

Non-Patent Citations (1)

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NATURE, vol. 559, JPN6025047812, 2018, ISSN: 0005738170 *

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CN116490606A (zh) 2023-07-25
EP4236969A4 (en) 2024-12-11
EP4236969A1 (en) 2023-09-06
WO2022094348A1 (en) 2022-05-05
US20230365997A1 (en) 2023-11-16

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