JP2023545830A5 - - Google Patents

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Publication number
JP2023545830A5
JP2023545830A5 JP2023523244A JP2023523244A JP2023545830A5 JP 2023545830 A5 JP2023545830 A5 JP 2023545830A5 JP 2023523244 A JP2023523244 A JP 2023523244A JP 2023523244 A JP2023523244 A JP 2023523244A JP 2023545830 A5 JP2023545830 A5 JP 2023545830A5
Authority
JP
Japan
Prior art keywords
therapeutic composition
composition according
raav
insect cells
particles
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023523244A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023545830A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/055243 external-priority patent/WO2022082017A2/en
Publication of JP2023545830A publication Critical patent/JP2023545830A/ja
Publication of JP2023545830A5 publication Critical patent/JP2023545830A5/ja
Pending legal-status Critical Current

Links

JP2023523244A 2020-10-15 2021-10-15 組換えアデノ随伴ウイルス組成物及びその生産方法 Pending JP2023545830A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063092179P 2020-10-15 2020-10-15
US63/092,179 2020-10-15
PCT/US2021/055243 WO2022082017A2 (en) 2020-10-15 2021-10-15 Recombinant adeno-associated virus compositions and methods for producing same

Publications (2)

Publication Number Publication Date
JP2023545830A JP2023545830A (ja) 2023-10-31
JP2023545830A5 true JP2023545830A5 (enExample) 2024-10-24

Family

ID=78819612

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023523244A Pending JP2023545830A (ja) 2020-10-15 2021-10-15 組換えアデノ随伴ウイルス組成物及びその生産方法

Country Status (10)

Country Link
US (1) US20220119843A1 (enExample)
EP (1) EP4229206A2 (enExample)
JP (1) JP2023545830A (enExample)
KR (1) KR20230088393A (enExample)
CN (1) CN116710567A (enExample)
AU (1) AU2021359852A1 (enExample)
CA (1) CA3198675A1 (enExample)
IL (1) IL302109A (enExample)
MX (1) MX2023004420A (enExample)
WO (1) WO2022082017A2 (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN120077057A (zh) 2022-10-04 2025-05-30 伊莱利利公司 Trem2相关疾病和病症的基因治疗
AR131035A1 (es) 2022-11-11 2025-02-12 Lilly Co Eli Ácidos nucleicos sintéticos que incluyen constructos promotores dirigidos a astrocitos y métodos de uso de los mismos
CN116350801A (zh) * 2022-11-22 2023-06-30 四川至善唯新生物科技有限公司 一种重组腺相关病毒载体的药物组合物及其用途
TW202432839A (zh) * 2022-12-06 2024-08-16 美商再生元醫藥公司 用於確定病毒載體基因體滴度之液滴式數位pcr分析
WO2025190864A1 (en) * 2024-03-11 2025-09-18 Sartorius Stedim Biotech Gmbh Improved cell lysis methods, reagents, and kits for viral vector release and production
WO2026043765A1 (en) 2024-08-21 2026-02-26 Eli Lilly And Company Engineered regulatory splice elements for gene therapies

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1463805B1 (en) 2001-12-17 2014-10-22 The Trustees of The University of Pennsylvania Adeno-associated virus (aav) serotype 9 sequences, vectors containing same, and uses therefor
WO2007084773A2 (en) * 2006-01-20 2007-07-26 University Of North Carolina At Chapel Hill Enhanced production of infectious parvovirus vectors in insect cells
EP3387138B2 (en) * 2015-12-11 2026-05-27 The Trustees Of The University Of Pennsylvania Scalable purification method for aav9
CN106916793B (zh) * 2015-12-24 2019-01-15 中国科学院武汉物理与数学研究所 一种重组腺相关病毒的制备方法及重组杆状病毒
US20200316221A1 (en) * 2016-10-13 2020-10-08 University Of Massachusetts Aav capsid designs
EP3692158A4 (en) * 2017-10-03 2021-08-04 Prevail Therapeutics, Inc. GENE THERAPIES FOR LYSOSOMAL DISEASES
MX2020004005A (es) 2017-10-03 2020-10-05 Prevail Therapeutics Inc Terapias genicas para los trastornos lisosomales.
CN111542549A (zh) 2017-10-03 2020-08-14 普利维尔治疗公司 用于溶酶体障碍的基因疗法
AU2018354195A1 (en) 2017-10-23 2020-06-04 Prevail Therapeutics, Inc. Gene therapies for neurodegenerative disease
EP4585229A3 (en) * 2017-11-08 2026-01-14 Novartis AG Means and method for preparing viral vectors and uses of same

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