JP2023543154A5 - - Google Patents

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Publication number
JP2023543154A5
JP2023543154A5 JP2023516514A JP2023516514A JP2023543154A5 JP 2023543154 A5 JP2023543154 A5 JP 2023543154A5 JP 2023516514 A JP2023516514 A JP 2023516514A JP 2023516514 A JP2023516514 A JP 2023516514A JP 2023543154 A5 JP2023543154 A5 JP 2023543154A5
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JP
Japan
Prior art keywords
nucleic acid
acid sequence
mammalian
seq
specific regulatory
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JP2023516514A
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English (en)
Japanese (ja)
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JP2023543154A (ja
JP7846677B2 (ja
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Priority claimed from PCT/US2021/049914 external-priority patent/WO2022056291A1/en
Publication of JP2023543154A publication Critical patent/JP2023543154A/ja
Publication of JP2023543154A5 publication Critical patent/JP2023543154A5/ja
Application granted granted Critical
Publication of JP7846677B2 publication Critical patent/JP7846677B2/ja
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JP2023516514A 2020-09-11 2021-09-10 筋特異的ハイブリッドプロモーター Active JP7846677B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063077339P 2020-09-11 2020-09-11
US63/077,339 2020-09-11
PCT/US2021/049914 WO2022056291A1 (en) 2020-09-11 2021-09-10 Muscle-specific hybrid promoter

Publications (3)

Publication Number Publication Date
JP2023543154A JP2023543154A (ja) 2023-10-13
JP2023543154A5 true JP2023543154A5 (https=) 2024-09-04
JP7846677B2 JP7846677B2 (ja) 2026-04-15

Family

ID=80629936

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023516514A Active JP7846677B2 (ja) 2020-09-11 2021-09-10 筋特異的ハイブリッドプロモーター

Country Status (6)

Country Link
US (1) US20230346976A1 (https=)
EP (1) EP4211251A4 (https=)
JP (1) JP7846677B2 (https=)
AU (1) AU2021342165A1 (https=)
CA (1) CA3192120A1 (https=)
WO (1) WO2022056291A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2026506177A (ja) 2023-02-21 2026-02-20 イリューコン セラピューティクス, インコーポレイテッド 改変インターロイキン2(il2)ポリペプチドをコードするポリヌクレオチド、ならびにその作製方法および使用方法
WO2024216118A1 (en) * 2023-04-14 2024-10-17 Precision Biosciences, Inc. Muscle-specific expression cassettes
WO2025157259A1 (en) * 2024-01-25 2025-07-31 Sichuan Real & Best Biotech Co., Ltd. Novel muscle-specific promoters
WO2025235807A1 (en) * 2024-05-10 2025-11-13 Solid Biosciences, Inc. Compositions and methods to improve graft survival

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1390490B1 (en) * 2001-05-24 2009-04-15 Genzyme Corporation Muscle-specific expression vectors
PL3097197T3 (pl) * 2014-01-21 2021-06-28 Vrije Universiteit Brussel Mięśniowo-specyficzne elementy regulatorowe kwasów nukleinowych oraz sposoby i ich zastosowanie
WO2018178067A1 (en) * 2017-03-27 2018-10-04 Vrije Universiteit Brussel Diaphragm-specific nucleic acid regulatory elements and methods and use thereof
EP3934700A4 (en) * 2019-03-06 2022-12-14 Generation Bio Co. NON-ACTIVE LIPID NANOPARTICLES WITH CAPSID-FREE, NON-VIRAL DNA

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