JP2023531718A5 - - Google Patents

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Publication number
JP2023531718A5
JP2023531718A5 JP2022579942A JP2022579942A JP2023531718A5 JP 2023531718 A5 JP2023531718 A5 JP 2023531718A5 JP 2022579942 A JP2022579942 A JP 2022579942A JP 2022579942 A JP2022579942 A JP 2022579942A JP 2023531718 A5 JP2023531718 A5 JP 2023531718A5
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JP
Japan
Prior art keywords
sequence
seq
polypeptide
homologous
sgrna
Prior art date
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Application number
JP2022579942A
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English (en)
Japanese (ja)
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JP7847778B2 (ja
JP2023531718A (ja
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Priority claimed from EP20382568.2A external-priority patent/EP3929294A1/en
Application filed filed Critical
Publication of JP2023531718A publication Critical patent/JP2023531718A/ja
Publication of JP2023531718A5 publication Critical patent/JP2023531718A5/ja
Application granted granted Critical
Publication of JP7847778B2 publication Critical patent/JP7847778B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2022579942A 2020-06-26 2021-06-28 ピルビン酸キナーゼ欠乏症（ｐｋｄ）遺伝子編集治療法 Active JP7847778B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP20382568.2 2020-06-26
EP20382568.2A EP3929294A1 (en) 2020-06-26 2020-06-26 Pyruvate kinase deficiency (pkd) gene editing treatment method
PCT/EP2021/067719 WO2021260227A1 (en) 2020-06-26 2021-06-28 Pyruvate kinase deficiency (pkd) gene editing treatment method

Publications (3)

Publication Number Publication Date
JP2023531718A JP2023531718A (ja) 2023-07-25
JP2023531718A5 true JP2023531718A5 (https=) 2024-07-09
JP7847778B2 JP7847778B2 (ja) 2026-04-20

Family

ID=71607853

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022579942A Active JP7847778B2 (ja) 2020-06-26 2021-06-28 ピルビン酸キナーゼ欠乏症（ｐｋｄ）遺伝子編集治療法

Country Status (9)

Country Link
US (1) US20230303990A1 (https=)
EP (2) EP3929294A1 (https=)
JP (1) JP7847778B2 (https=)
KR (1) KR20230029922A (https=)
CN (1) CN116648511A (https=)
AU (1) AU2021298186A1 (https=)
CA (1) CA3188164A1 (https=)
MX (1) MX2023000035A (https=)
WO (1) WO2021260227A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4534654A1 (en) * 2023-10-02 2025-04-09 Consorcio Centro de Investigación Biomédica en Red Pre-stimulation method of cd34+ cells to achieve clinically relevant gene editing frequencies

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