JP2023530379A5 - - Google Patents

Info

Publication number
JP2023530379A5
JP2023530379A5 JP2022547232A JP2022547232A JP2023530379A5 JP 2023530379 A5 JP2023530379 A5 JP 2023530379A5 JP 2022547232 A JP2022547232 A JP 2022547232A JP 2022547232 A JP2022547232 A JP 2022547232A JP 2023530379 A5 JP2023530379 A5 JP 2023530379A5
Authority
JP
Japan
Prior art keywords
nucleic acid
rna
acid molecule
circrna
molecule according
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022547232A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023530379A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/025463 external-priority patent/WO2021159129A2/en
Publication of JP2023530379A publication Critical patent/JP2023530379A/ja
Publication of JP2023530379A5 publication Critical patent/JP2023530379A5/ja
Pending legal-status Critical Current

Links

JP2022547232A 2020-02-04 2021-04-01 環状rna発現のための組成物および方法 Pending JP2023530379A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202062969758P 2020-02-04 2020-02-04
US62/969,758 2020-02-04
PCT/US2021/025463 WO2021159129A2 (en) 2020-02-04 2021-04-01 Compositions and methods for circular rna expression

Publications (2)

Publication Number Publication Date
JP2023530379A JP2023530379A (ja) 2023-07-18
JP2023530379A5 true JP2023530379A5 (https=) 2024-04-08

Family

ID=77199626

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022547232A Pending JP2023530379A (ja) 2020-02-04 2021-04-01 環状rna発現のための組成物および方法

Country Status (6)

Country Link
US (1) US12600987B2 (https=)
EP (1) EP4100523A4 (https=)
JP (1) JP2023530379A (https=)
AU (1) AU2021216593A1 (https=)
CA (1) CA3168840A1 (https=)
WO (1) WO2021159129A2 (https=)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
MX2024003262A (es) 2021-09-17 2024-06-19 Flagship Pioneering Innovations Vi Llc Composiciones y metodos para producir poliribonucleotidos circulares.
JP2026500226A (ja) * 2022-12-07 2026-01-06 サーキヨ・アクチエボラグ circRNA発現コンストラクト
CN121241137A (zh) * 2023-05-24 2025-12-30 南京金斯瑞生物科技有限公司 用于制备环状rna的载体和方法

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ITRM20020253A1 (it) 2002-05-08 2003-11-10 Univ Roma Molecole chimeriche di snrna con sequenze antisenso per le giunzioni di splicing del gene della distrofina e applicazioni terapeutiche.
FR2874384B1 (fr) 2004-08-17 2010-07-30 Genethon Vecteur viral adeno-associe pour realiser du saut d'exons dans un gene codant une proteine a domaines dispensables
CN107447033B (zh) 2017-09-15 2020-11-17 东南大学 一种结直肠癌诊断生物标志物及其应用
JP7385282B2 (ja) * 2017-11-07 2023-11-22 ザ・ユニヴァーシティ・オヴ・ノース・キャロライナ・アト・チャペル・ヒル 環状rna分子のための方法及び組成物

Similar Documents

Publication Publication Date Title
JP2022544412A5 (https=)
US9458459B2 (en) Methods for enhancing utrophin production via inhibition of microRNA
AU2013248981B2 (en) Mirna modulators of thermogenesis
JP2023530379A5 (https=)
CN104583400A (zh) 用于调节pten表达的组合物和方法
CN104602714A (zh) 用于调节bdnf表达的组合物和方法
CN104582737A (zh) 用于调节apoa1和abca1表达的组合物和方法
JP2025524740A (ja) オリゴヌクレオチド送達増強剤、医薬組成物およびそれらを使用する方法
WO2019204451A1 (en) Enhanced lipid nanoparticle drug delivery using a negatively charged polymer
CN111918968A (zh) Micro-RNA 22的抑制剂
JP2023506546A (ja) B型肝炎ウイルス感染症を処置するためのsept9阻害剤の使用
WO2022206739A1 (zh) 一种基于病毒载体的rna递送系统及其应用
EP4269585A1 (en) Guide rna for editing polyadenylation signal sequence of target rna
JP2023506540A (ja) B型肝炎ウイルス感染を処置するためのscamp3阻害剤の使用
EP4265724A1 (en) Rnai agent for inhibiting hbv expression and use thereof
KR101168726B1 (ko) 암 치료용 약학 조성물
JP2025094072A (ja) B型肝炎ウイルス感染を処置するためのcops3阻害剤の使用
WO2024002045A1 (en) Oligonucleotide delivery agents, pharmaceutical compositions and methods using the same
Riasi et al. Effect of Intramuscular and Intraperitoneal Injections of conjugated MSTN-siRNA-cholesterol on Inhibition of Myostatin Gene expression.
AU2020349991A1 (en) Nucleic acid molecule for treating immune thrombocytopenia and application thereof
JP2023506954A (ja) B型肝炎ウイルス感染を処置するためのsaraf阻害剤の使用
CN118202046A (zh) 具有降低的脱靶效应的经修饰的小干扰rna分子
WO2022206778A1 (zh) 一种用于治疗肺纤维化的rna质粒递送系统
WO2022206784A1 (zh) 一种用于治疗肺纤维化的rna递送系统
JP2023506550A (ja) B型肝炎ウイルス感染症を処置するためのsbds阻害剤の使用