JP2023528435A5 - - Google Patents
Info
- Publication number
- JP2023528435A5 JP2023528435A5 JP2022574357A JP2022574357A JP2023528435A5 JP 2023528435 A5 JP2023528435 A5 JP 2023528435A5 JP 2022574357 A JP2022574357 A JP 2022574357A JP 2022574357 A JP2022574357 A JP 2022574357A JP 2023528435 A5 JP2023528435 A5 JP 2023528435A5
- Authority
- JP
- Japan
- Prior art keywords
- oligonucleotide
- spacer
- bond
- optionally
- seq
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063033926P | 2020-06-03 | 2020-06-03 | |
| US63/033,926 | 2020-06-03 | ||
| US202063119717P | 2020-12-01 | 2020-12-01 | |
| US63/119,717 | 2020-12-01 | ||
| PCT/US2021/035603 WO2021247800A2 (en) | 2020-06-03 | 2021-06-03 | Treatment of neurological diseases using modulators of gene transcripts |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023528435A JP2023528435A (ja) | 2023-07-04 |
| JP2023528435A5 true JP2023528435A5 (OSRAM) | 2024-06-10 |
Family
ID=78831722
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022574357A Pending JP2023528435A (ja) | 2020-06-03 | 2021-06-03 | 遺伝子転写物のモジュレーターを使用する神経学的疾患の処置 |
Country Status (8)
| Country | Link |
|---|---|
| US (1) | US20230235332A1 (OSRAM) |
| EP (1) | EP4162051A4 (OSRAM) |
| JP (1) | JP2023528435A (OSRAM) |
| KR (1) | KR20230043819A (OSRAM) |
| AU (1) | AU2021284360A1 (OSRAM) |
| CA (1) | CA3185488A1 (OSRAM) |
| IL (1) | IL298647A (OSRAM) |
| WO (1) | WO2021247800A2 (OSRAM) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| GB202208387D0 (en) * | 2022-06-08 | 2022-07-20 | Ucl Business Ltd | Modified U7 snRNA construct |
| WO2026080323A1 (en) | 2024-10-09 | 2026-04-16 | Quralis Corporation | Treatment of neurological diseases using modulators of unc13a gene transcripts |
Family Cites Families (7)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO1998013527A2 (en) * | 1996-09-24 | 1998-04-02 | Rapigene, Inc. | Compositions and methods for enhancing hybridization specificity |
| WO2006017522A2 (en) * | 2004-08-03 | 2006-02-16 | University Of Utah Research Foundation | Use of antisense oligonucleotides to effect translation modulation |
| AU2011325956B2 (en) * | 2010-11-12 | 2016-07-14 | The General Hospital Corporation | Polycomb-associated non-coding RNAs |
| US11833168B2 (en) * | 2018-06-14 | 2023-12-05 | Ionis Pharmaceuticals, Inc. | Compounds and methods for increasing STMN2 expression |
| CN114173821A (zh) * | 2019-01-14 | 2022-03-11 | 哈佛学院校长同事会 | 用于恢复stmn2水平的方法和组合物 |
| JP7795914B2 (ja) * | 2019-06-03 | 2026-01-08 | クラリス コーポレーション | 神経学的疾患を処置するためのオリゴヌクレオチドおよびその使用方法 |
| EP4127172A4 (en) * | 2020-03-25 | 2025-06-04 | President and Fellows of Harvard College | Methods and compositions for restoring STMN2 levels |
-
2021
- 2021-06-03 KR KR1020237000041A patent/KR20230043819A/ko active Pending
- 2021-06-03 AU AU2021284360A patent/AU2021284360A1/en active Pending
- 2021-06-03 CA CA3185488A patent/CA3185488A1/en active Pending
- 2021-06-03 US US17/928,708 patent/US20230235332A1/en active Pending
- 2021-06-03 EP EP21817154.4A patent/EP4162051A4/en active Pending
- 2021-06-03 WO PCT/US2021/035603 patent/WO2021247800A2/en not_active Ceased
- 2021-06-03 JP JP2022574357A patent/JP2023528435A/ja active Pending
- 2021-06-03 IL IL298647A patent/IL298647A/en unknown
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