JP2023515664A - 修飾された短い干渉核酸(siNA)分子およびそれらの使用 - Google Patents

修飾された短い干渉核酸(siNA)分子およびそれらの使用 Download PDF

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JP2023515664A
JP2023515664A JP2022552538A JP2022552538A JP2023515664A JP 2023515664 A JP2023515664 A JP 2023515664A JP 2022552538 A JP2022552538 A JP 2022552538A JP 2022552538 A JP2022552538 A JP 2022552538A JP 2023515664 A JP2023515664 A JP 2023515664A
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nucleotides
sina
nucleotide sequence
nucleotide
methyl
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JP2023515664A5 (enExample
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バイゲルマン,レオニード
クマール ラジワンシ,ヴィヴェク
ホスバッハ,マルクス
ケー. パンデイ,ラジェンドラ
ホン,ジン
エルテプ,ラクスマン
マルティネス モンテロ,サウル
コスタ,エヌ.ティラニ エス. デ
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アリゴス セラピューティクス,インコーポレーテッド
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JP2022552538A 2020-03-06 2021-03-05 修飾された短い干渉核酸(siNA)分子およびそれらの使用 Pending JP2023515664A (ja)

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US62/986,150 2020-03-06
US202063109196P 2020-11-03 2020-11-03
US63/109,196 2020-11-03
PCT/US2021/021199 WO2021178885A1 (en) 2020-03-06 2021-03-05 Modified short interfering nucleic acid (sina) molecules and uses thereof

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