JP2023512783A5 - - Google Patents

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Publication number
JP2023512783A5
JP2023512783A5 JP2022547874A JP2022547874A JP2023512783A5 JP 2023512783 A5 JP2023512783 A5 JP 2023512783A5 JP 2022547874 A JP2022547874 A JP 2022547874A JP 2022547874 A JP2022547874 A JP 2022547874A JP 2023512783 A5 JP2023512783 A5 JP 2023512783A5
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JP
Japan
Prior art keywords
approximately
gaa
use according
individual
oligosaccharide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2022547874A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023512783A (ja
JP7804582B2 (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/017113 external-priority patent/WO2021159092A1/en
Publication of JP2023512783A publication Critical patent/JP2023512783A/ja
Publication of JP2023512783A5 publication Critical patent/JP2023512783A5/ja
Priority to JP2025138630A priority Critical patent/JP2025166240A/ja
Application granted granted Critical
Publication of JP7804582B2 publication Critical patent/JP7804582B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

Links

JP2022547874A 2020-02-08 2021-02-08 ポンペ病を処置するための組成物および方法 Active JP7804582B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025138630A JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202062971930P 2020-02-08 2020-02-08
US62/971,930 2020-02-08
US202063115975P 2020-11-19 2020-11-19
US63/115,975 2020-11-19
PCT/US2021/017113 WO2021159092A1 (en) 2020-02-08 2021-02-08 Compositions and methods for treating pompe disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025138630A Division JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Publications (3)

Publication Number Publication Date
JP2023512783A JP2023512783A (ja) 2023-03-29
JP2023512783A5 true JP2023512783A5 (enExample) 2024-02-16
JP7804582B2 JP7804582B2 (ja) 2026-01-22

Family

ID=74853758

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022547874A Active JP7804582B2 (ja) 2020-02-08 2021-02-08 ポンペ病を処置するための組成物および方法
JP2025138630A Pending JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025138630A Pending JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Country Status (12)

Country Link
US (2) US12251430B2 (enExample)
EP (1) EP4100120A1 (enExample)
JP (2) JP7804582B2 (enExample)
KR (1) KR20220139936A (enExample)
CN (1) CN115715218A (enExample)
AU (1) AU2021216055A1 (enExample)
BR (1) BR112022015505A2 (enExample)
CA (1) CA3167091A1 (enExample)
IL (1) IL295415A (enExample)
MX (1) MX2022009753A (enExample)
WO (1) WO2021159092A1 (enExample)
ZA (1) ZA202209925B (enExample)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL295415A (en) 2020-02-08 2022-10-01 Genzyme Corp Compositions and methods for treating pompe disease
CN115916245A (zh) 2020-06-14 2023-04-04 建新公司 用于治疗晚发型庞贝病的组合物和方法

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7723296B2 (en) * 2001-01-18 2010-05-25 Genzyme Corporation Methods for introducing mannose-6-phosphate and other oligosaccharides onto glycoproteins and its application thereof
WO2006108052A2 (en) 2005-04-06 2006-10-12 Genzyme Corporation Peg and polysialic lysosomal enzyme conjugates via acid labile linkers for therapeutic targeting
CN102978185B (zh) * 2007-01-18 2015-02-11 建新公司 包含氨基氧基基团的寡糖及其轭合物
PL2889043T3 (pl) 2008-12-16 2019-09-30 Genzyme Corporation Syntetyczne związki pośrednie do wytwarzania koniugatów oligosacharyd-białko
MX2013013445A (es) 2011-05-16 2014-07-28 Genzyme Corp Induccion de tolerancia inmunologica utilizando metotrexato.
WO2016149508A1 (en) * 2015-03-19 2016-09-22 Shire Human Genetic Therapies, Inc. Mrna therapy for pompe disease
KR102747683B1 (ko) * 2015-12-30 2024-12-31 아미쿠스 세라퓨틱스, 인코포레이티드 폼페병 치료용의 강화된 산 알파-글루코시다제
IL295415A (en) 2020-02-08 2022-10-01 Genzyme Corp Compositions and methods for treating pompe disease

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