JP2023512783A5 - - Google Patents

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Publication number
JP2023512783A5
JP2023512783A5 JP2022547874A JP2022547874A JP2023512783A5 JP 2023512783 A5 JP2023512783 A5 JP 2023512783A5 JP 2022547874 A JP2022547874 A JP 2022547874A JP 2022547874 A JP2022547874 A JP 2022547874A JP 2023512783 A5 JP2023512783 A5 JP 2023512783A5
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JP
Japan
Prior art keywords
approximately
gaa
use according
individual
oligosaccharide
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2022547874A
Other languages
English (en)
Japanese (ja)
Other versions
JP7804582B2 (ja
JP2023512783A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/017113 external-priority patent/WO2021159092A1/en
Publication of JP2023512783A publication Critical patent/JP2023512783A/ja
Publication of JP2023512783A5 publication Critical patent/JP2023512783A5/ja
Priority to JP2025138630A priority Critical patent/JP2025166240A/ja
Application granted granted Critical
Publication of JP7804582B2 publication Critical patent/JP7804582B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2022547874A 2020-02-08 2021-02-08 ポンペ病を処置するための組成物および方法 Active JP7804582B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2025138630A JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US202062971930P 2020-02-08 2020-02-08
US62/971,930 2020-02-08
US202063115975P 2020-11-19 2020-11-19
US63/115,975 2020-11-19
PCT/US2021/017113 WO2021159092A1 (en) 2020-02-08 2021-02-08 Compositions and methods for treating pompe disease

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2025138630A Division JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Publications (3)

Publication Number Publication Date
JP2023512783A JP2023512783A (ja) 2023-03-29
JP2023512783A5 true JP2023512783A5 (cg-RX-API-DMAC10.html) 2024-02-16
JP7804582B2 JP7804582B2 (ja) 2026-01-22

Family

ID=74853758

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2022547874A Active JP7804582B2 (ja) 2020-02-08 2021-02-08 ポンペ病を処置するための組成物および方法
JP2025138630A Pending JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2025138630A Pending JP2025166240A (ja) 2020-02-08 2025-08-22 ポンペ病を処置するための組成物および方法

Country Status (13)

Country Link
US (2) US12251430B2 (cg-RX-API-DMAC10.html)
EP (1) EP4100120A1 (cg-RX-API-DMAC10.html)
JP (2) JP7804582B2 (cg-RX-API-DMAC10.html)
KR (1) KR20220139936A (cg-RX-API-DMAC10.html)
CN (1) CN115715218A (cg-RX-API-DMAC10.html)
AU (1) AU2021216055A1 (cg-RX-API-DMAC10.html)
BR (1) BR112022015505A2 (cg-RX-API-DMAC10.html)
CA (1) CA3167091A1 (cg-RX-API-DMAC10.html)
IL (1) IL295415A (cg-RX-API-DMAC10.html)
MX (1) MX2022009753A (cg-RX-API-DMAC10.html)
TW (1) TWI917351B (cg-RX-API-DMAC10.html)
WO (1) WO2021159092A1 (cg-RX-API-DMAC10.html)
ZA (1) ZA202209925B (cg-RX-API-DMAC10.html)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4100120A1 (en) 2020-02-08 2022-12-14 Genzyme Corporation Compositions and methods for treating pompe disease
BR112022025314A2 (pt) 2020-06-14 2023-01-03 Genzyme Corp Composições e métodos para tratamento de doença de pompe de início tardio

Family Cites Families (8)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US7723296B2 (en) 2001-01-18 2010-05-25 Genzyme Corporation Methods for introducing mannose-6-phosphate and other oligosaccharides onto glycoproteins and its application thereof
JP5137814B2 (ja) 2005-04-06 2013-02-06 ジェンザイム・コーポレーション 治療ターゲティングのための酸不安定リンカーを介するpegおよびポリシアルリソソーム酵素のコンジュゲート
CN102978185B (zh) * 2007-01-18 2015-02-11 建新公司 包含氨基氧基基团的寡糖及其轭合物
EP3608330B1 (en) * 2008-12-16 2022-11-09 Genzyme Corporation Synthetic intermediates for preparing oligosaccharide-protein conjugates
AU2012256281B2 (en) 2011-05-16 2017-06-15 Genzyme Corporation Induction of immune tolerance by using methotrexate
EP3270894B1 (en) * 2015-03-19 2021-02-24 Translate Bio, Inc. Mrna therapy for pompe disease
IL299470B2 (en) * 2015-12-30 2026-05-01 Amicus Therapeutics Inc Improved acid alpha-glucosidase for the treatment of Pompe disease
EP4100120A1 (en) 2020-02-08 2022-12-14 Genzyme Corporation Compositions and methods for treating pompe disease

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