JP2022532802A5 - - Google Patents
Info
- Publication number
- JP2022532802A5 JP2022532802A5 JP2021569298A JP2021569298A JP2022532802A5 JP 2022532802 A5 JP2022532802 A5 JP 2022532802A5 JP 2021569298 A JP2021569298 A JP 2021569298A JP 2021569298 A JP2021569298 A JP 2021569298A JP 2022532802 A5 JP2022532802 A5 JP 2022532802A5
- Authority
- JP
- Japan
- Prior art keywords
- expression cassette
- transfer plasmid
- tcirg1
- ltr
- lentivirus
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025005848A JP2025063200A (ja) | 2019-05-23 | 2025-01-16 | 乳児性悪性大理石骨病に対する遺伝子療法ベクター |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962852216P | 2019-05-23 | 2019-05-23 | |
| US62/852,216 | 2019-05-23 | ||
| PCT/US2020/034394 WO2020237219A1 (en) | 2019-05-23 | 2020-05-22 | Gene therapy vectors for infantile malignant osteopetrosis |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025005848A Division JP2025063200A (ja) | 2019-05-23 | 2025-01-16 | 乳児性悪性大理石骨病に対する遺伝子療法ベクター |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022532802A JP2022532802A (ja) | 2022-07-19 |
| JP2022532802A5 true JP2022532802A5 (https=) | 2023-05-25 |
| JP7623299B2 JP7623299B2 (ja) | 2025-01-28 |
Family
ID=73458718
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021569298A Active JP7623299B2 (ja) | 2019-05-23 | 2020-05-22 | 乳児性悪性大理石骨病に対する遺伝子療法ベクター |
| JP2025005848A Pending JP2025063200A (ja) | 2019-05-23 | 2025-01-16 | 乳児性悪性大理石骨病に対する遺伝子療法ベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025005848A Pending JP2025063200A (ja) | 2019-05-23 | 2025-01-16 | 乳児性悪性大理石骨病に対する遺伝子療法ベクター |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220218844A1 (https=) |
| EP (1) | EP3973066A4 (https=) |
| JP (2) | JP7623299B2 (https=) |
| KR (1) | KR20220012266A (https=) |
| CN (1) | CN113994008A (https=) |
| AU (1) | AU2020278046A1 (https=) |
| BR (1) | BR112021023473A2 (https=) |
| CA (1) | CA3137700A1 (https=) |
| IL (1) | IL288193A (https=) |
| MX (1) | MX2021014337A (https=) |
| SG (1) | SG11202112347RA (https=) |
| WO (1) | WO2020237219A1 (https=) |
Families Citing this family (6)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HUE055862T2 (hu) | 2016-04-20 | 2021-12-28 | Centro De Investig Energeticas | Készítmények és eljárások PKLR fokozott génexpressziójára |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| WO2019200167A1 (en) | 2018-04-11 | 2019-10-17 | Rocket Pharmaceuticals, Ltd. | Compositions and methods for stem cell transplant |
| MX2020011386A (es) | 2018-04-27 | 2021-01-29 | Spacecraft Seven Llc | Terapia genica para la degeneracion del snc. |
| KR20230043869A (ko) | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| CN116042719B (zh) * | 2022-12-28 | 2025-11-11 | 蓝图生物医药(广州)有限公司 | 一种重组腺相关病毒载体及其应用 |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5994136A (en) | 1997-12-12 | 1999-11-30 | Cell Genesys, Inc. | Method and means for producing high titer, safe, recombinant lentivirus vectors |
| GB0202771D0 (en) * | 2002-02-06 | 2002-03-27 | Univ Aberdeen | Genetic markers for bone mass |
| CA2650507A1 (en) * | 2006-04-27 | 2007-11-08 | Universite De Montreal | Assessment and reduction of risk of graft-versus-host disease |
| AU2013309488A1 (en) * | 2012-08-29 | 2015-03-05 | Nature Technology Corporation | DNA plasmids with improved expression |
| WO2014077863A1 (en) * | 2012-11-19 | 2014-05-22 | Nature Technology Corporation | Replicative minicircle vectors with improved expression |
| MX374532B (es) * | 2013-06-17 | 2025-03-06 | Broad Inst Inc | Suministro, uso y aplicaciones terapéuticas de los sistemas y composiciones crispr-cas, para actuar sobre trastornos y enfermedades utilizando componentes víricos. |
| CN116064678A (zh) * | 2016-01-15 | 2023-05-05 | 美国基因技术国际有限公司 | 用于活化γ-δT细胞的方法和组合物 |
| CN121102467A (zh) * | 2016-04-22 | 2025-12-12 | 克莱格医学有限公司 | 用于细胞免疫疗法的组合物和方法 |
| KR20240151726A (ko) | 2016-09-08 | 2024-10-18 | 센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피. | 판코니 빈혈 환자를 위한 유전자 치료 |
-
2020
- 2020-05-22 SG SG11202112347RA patent/SG11202112347RA/en unknown
- 2020-05-22 CA CA3137700A patent/CA3137700A1/en active Pending
- 2020-05-22 AU AU2020278046A patent/AU2020278046A1/en not_active Abandoned
- 2020-05-22 JP JP2021569298A patent/JP7623299B2/ja active Active
- 2020-05-22 BR BR112021023473A patent/BR112021023473A2/pt unknown
- 2020-05-22 US US17/612,134 patent/US20220218844A1/en not_active Abandoned
- 2020-05-22 CN CN202080044921.1A patent/CN113994008A/zh active Pending
- 2020-05-22 MX MX2021014337A patent/MX2021014337A/es unknown
- 2020-05-22 KR KR1020217040611A patent/KR20220012266A/ko not_active Ceased
- 2020-05-22 EP EP20809375.7A patent/EP3973066A4/en active Pending
- 2020-05-22 WO PCT/US2020/034394 patent/WO2020237219A1/en not_active Ceased
-
2021
- 2021-11-17 IL IL288193A patent/IL288193A/en unknown
-
2025
- 2025-01-16 JP JP2025005848A patent/JP2025063200A/ja active Pending
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