JP2022508835A - 眼咽頭筋ジストロフィー（ｏｐｍｄ）を治療するための方法 - Google Patents

眼咽頭筋ジストロフィー（ｏｐｍｄ）を治療するための方法 Download PDF

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JP2022508835A
JP2022508835A JP2021546400A JP2021546400A JP2022508835A JP 2022508835 A JP2022508835 A JP 2022508835A JP 2021546400 A JP2021546400 A JP 2021546400A JP 2021546400 A JP2021546400 A JP 2021546400A JP 2022508835 A JP2022508835 A JP 2022508835A
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shmir
nucleic acid
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JPWO2020077412A5 (enExample
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ストリングス－ウフォムバー，ヴァネッサ
スーイ，デイヴィッド
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ベニテック バイオファーマ リミテッド
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JP2021546400A 2018-10-17 2019-10-17 眼咽頭筋ジストロフィー（ｏｐｍｄ）を治療するための方法 Pending JP2022508835A (ja)

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Application Number Priority Date Filing Date Title
US201862747089P 2018-10-17 2018-10-17
US62/747,089 2018-10-17
PCT/AU2019/051134 WO2020077412A1 (en) 2018-10-17 2019-10-17 Methods for treating oculopharyngeal muscular dystrophy (opmd)

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JP2022508835A true JP2022508835A (ja) 2022-01-19
JPWO2020077412A5 JPWO2020077412A5 (enExample) 2022-10-24

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US (1) US20220106594A1 (enExample)
EP (1) EP3866859A4 (enExample)
JP (1) JP2022508835A (enExample)
KR (1) KR20210081361A (enExample)
CN (1) CN112867511A (enExample)
AU (1) AU2019362925A1 (enExample)
BR (1) BR112021007256A2 (enExample)
CA (1) CA3114945A1 (enExample)
IL (1) IL282323A (enExample)
MX (1) MX2021004225A (enExample)
SG (1) SG11202102185RA (enExample)
WO (1) WO2020077412A1 (enExample)

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CN115838725B (zh) * 2022-12-30 2023-09-08 广州派真生物技术有限公司 在哺乳动物心脏中特异性启动基因的启动子序列及其应用

Citations (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2018107228A1 (en) * 2016-12-14 2018-06-21 Benitec Biopharma Limited Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof

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* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2014117050A2 (en) * 2013-01-26 2014-07-31 Mirimus, Inc. Modified mirna as a scaffold for shrna
KR102353847B1 (ko) * 2016-04-14 2022-01-21 베니텍 바이오파마 리미티드 안구인두 근이영양증(opmd)의 치료용 시약 및 이의 용도
EP3931317A4 (en) * 2019-02-28 2023-01-04 Benitec IP Holdings Inc. COMPOSITIONS AND METHODS FOR TREATMENT OF OCULOPHARYNGEAL MUSCULAR DYSTROPHY (OPMD)

Patent Citations (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2018107228A1 (en) * 2016-12-14 2018-06-21 Benitec Biopharma Limited Reagents for treatment of oculopharyngeal muscular dystrophy (opmd) and use thereof

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SG11202102185RA (en) 2021-05-28
US20220106594A1 (en) 2022-04-07
BR112021007256A2 (pt) 2021-08-10
MX2021004225A (es) 2021-05-27
WO2020077412A1 (en) 2020-04-23
EP3866859A4 (en) 2023-08-09
AU2019362925A1 (en) 2021-05-06
KR20210081361A (ko) 2021-07-01
EP3866859A1 (en) 2021-08-25
CN112867511A (zh) 2021-05-28
CA3114945A1 (en) 2020-04-23
IL282323A (en) 2021-05-31

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