JP2018531965A5 - - Google Patents
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- JP2018531965A5 JP2018531965A5 JP2018521617A JP2018521617A JP2018531965A5 JP 2018531965 A5 JP2018531965 A5 JP 2018531965A5 JP 2018521617 A JP2018521617 A JP 2018521617A JP 2018521617 A JP2018521617 A JP 2018521617A JP 2018531965 A5 JP2018531965 A5 JP 2018531965A5
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- pharmaceutically acceptable
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022087580A JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562248163P | 2015-10-29 | 2015-10-29 | |
| US62/248,163 | 2015-10-29 | ||
| PCT/US2016/059697 WO2017075580A1 (en) | 2015-10-29 | 2016-10-31 | Compositions and methods for treatment of peroxisomal disorders and leukodystrophies |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022087580A Division JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018531965A JP2018531965A (ja) | 2018-11-01 |
| JP2018531965A5 true JP2018531965A5 (https=) | 2019-12-12 |
| JP7088473B2 JP7088473B2 (ja) | 2022-06-21 |
Family
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Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018521617A Active JP7088473B2 (ja) | 2015-10-29 | 2016-10-31 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
| JP2022087580A Pending JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022087580A Pending JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (2) | US20170119899A1 (https=) |
| EP (1) | EP3368088B1 (https=) |
| JP (2) | JP7088473B2 (https=) |
| CN (1) | CN108430514B (https=) |
| AU (1) | AU2016343855B2 (https=) |
| CA (1) | CA3003589C (https=) |
| WO (1) | WO2017075580A1 (https=) |
Families Citing this family (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CA2957721C (en) * | 2014-08-13 | 2021-04-13 | The Johns Hopkins University | Selective dendrimer delivery to brain tumors |
| AU2018258654B2 (en) | 2017-04-27 | 2022-01-06 | The Johns Hopkins University | Dendrimer compositions for use in angiography |
| WO2018208707A1 (en) * | 2017-05-08 | 2018-11-15 | Neurovia, Inc. | Methods and compositions for treating demyelinating diseases |
| EP3707193A1 (en) | 2017-11-10 | 2020-09-16 | The Johns Hopkins University | Dendrimer delivery system and methods of use thereof |
| WO2019118951A2 (en) * | 2017-12-15 | 2019-06-20 | Duke University | Compositions and methods of enhancing the homing and/or engraftment of hematopoietic cells in the central nervous system |
| US20220072019A1 (en) * | 2018-10-19 | 2022-03-10 | Disarm Therapeutics, Inc. | Inhibitors of sarm1 in combination with nad+ or a nad+ precursor |
| WO2020142373A1 (en) * | 2019-01-02 | 2020-07-09 | Mayo Foundation For Medical Education And Research | Methods and materials for treating leukodystrophies |
| JP7759322B2 (ja) | 2019-12-04 | 2025-10-23 | アシュバッタ セラピューティクス， インコーポレイテッド | 眼に薬物送達するためのデンドリマー組成物および方法 |
| IL297531A (en) * | 2020-04-24 | 2022-12-01 | Ashvattha Therapeutics Inc | Dendrimer preparations and methods for treating severe acute respiratory distress syndrome |
| CA3189682A1 (en) * | 2020-07-17 | 2022-01-20 | Ashvattha Therapeutics, Inc. | Dendrimer compositions and methods for drug delivery to injured kidney |
| EP4426847A4 (en) * | 2021-11-04 | 2026-02-25 | Childrens Hospital Philadelphia | Compositions and methods for the treatment of metachromatic leukodystrophy and related disorders |
| US20260103728A1 (en) * | 2022-10-12 | 2026-04-16 | The Johns Hopkins University | Method of treating lbsl by enhancing dars2 expression |
| CN116082153A (zh) * | 2022-12-09 | 2023-05-09 | 长沙贝塔医药科技有限公司 | 一种丙烯酸酯类衍生物-13c的制备方法 |
| EP4410284A1 (en) * | 2023-02-02 | 2024-08-07 | Apteeus | Compound and method for the treatment of zellweger spectrum disorder |
| CN117643581A (zh) * | 2023-11-29 | 2024-03-05 | 徐州医科大学 | 白藜芦醇在制备激活sirt1基因的药物中的应用 |
| WO2025240286A1 (en) * | 2024-05-14 | 2025-11-20 | Washington State University | Neuron targeted 2-deoxyglucose dendrimer for imaging and treatment of neurological diseases |
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| ES2157422T3 (es) | 1995-02-07 | 2001-08-16 | Brusilow Entpr Llc | Trigliceridos y esteres etilicos de acido fenilalcanoico y acido fenilalquenoico utiles en el tratamiento de diversos trastornos. |
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| US8148356B2 (en) | 2005-08-24 | 2012-04-03 | Cumberland Pharmaceuticals, Inc. | Acetylcysteine composition and uses therefor |
| TW200817369A (en) * | 2006-05-22 | 2008-04-16 | Elan Pharm Inc | Preparation of polymer conjugates of therapeutic, agricultural and food additive compounds |
| JP5484339B2 (ja) | 2007-10-05 | 2014-05-07 | ウェイン ステート ユニバーシティー | 合成物の持続的な放出のためのデンドリマー |
| PL3133396T3 (pl) | 2008-04-29 | 2019-03-29 | Horizon Therapeutics, Llc | Sposób leczenia z zastosowaniem leków wychwytujących amoniak |
| WO2009142754A1 (en) * | 2008-05-22 | 2009-11-26 | Goverment Of The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Dendritic conjugates and methods of use |
| WO2010147831A1 (en) * | 2009-06-15 | 2010-12-23 | Wayne State University | Dendrimer based nanodevices for therapeutic and imaging purposes |
| MY173215A (en) | 2010-07-21 | 2020-01-06 | Cumberland Pharmaceuticals Inc | Acetylcysteine compositions and methods of use thereof |
| DK2760479T3 (en) | 2011-09-30 | 2017-07-17 | Horizon Therapeutics Llc | Nitrogen-removing drug for use in a method of treating a nitrogen retention disorder |
| WO2014178892A1 (en) * | 2013-05-03 | 2014-11-06 | Scanlan Thomas S | Use of sobetirome in the treatment of x-linked adrenolenoleukodystrophy |
| EP3019184A4 (en) * | 2013-06-07 | 2017-04-05 | The Administrators of the Tulane Educational Fund | Analogs of pituitary adenylate cyclase-activating polypeptide (pacap) and methods for their use |
| EP3036004B1 (en) | 2013-08-21 | 2022-12-07 | Concordia University | Dendrimer-resveratrol complex |
| AU2015301579B2 (en) * | 2014-08-13 | 2018-08-09 | Kennedy Krieger Institute, Inc. | Dendrimer compositions and use in treatment of neurological and CNS disorders |
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