JP2018531965A5 - - Google Patents
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- JP2018531965A5 JP2018531965A5 JP2018521617A JP2018521617A JP2018531965A5 JP 2018531965 A5 JP2018531965 A5 JP 2018531965A5 JP 2018521617 A JP2018521617 A JP 2018521617A JP 2018521617 A JP2018521617 A JP 2018521617A JP 2018531965 A5 JP2018531965 A5 JP 2018531965A5
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- pharmaceutically acceptable
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Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2022087580A JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562248163P | 2015-10-29 | 2015-10-29 | |
| US62/248,163 | 2015-10-29 | ||
| PCT/US2016/059697 WO2017075580A1 (en) | 2015-10-29 | 2016-10-31 | Compositions and methods for treatment of peroxisomal disorders and leukodystrophies |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022087580A Division JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2018531965A JP2018531965A (ja) | 2018-11-01 |
| JP2018531965A5 true JP2018531965A5 (https=) | 2019-12-12 |
| JP7088473B2 JP7088473B2 (ja) | 2022-06-21 |
Family
ID=57233968
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2018521617A Active JP7088473B2 (ja) | 2015-10-29 | 2016-10-31 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
| JP2022087580A Pending JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022087580A Pending JP2022105767A (ja) | 2015-10-29 | 2022-05-30 | ペルオキシソーム障害および白質ジストロフィーの処置のための組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (2) | US20170119899A1 (https=) |
| EP (1) | EP3368088B1 (https=) |
| JP (2) | JP7088473B2 (https=) |
| CN (1) | CN108430514B (https=) |
| AU (1) | AU2016343855B2 (https=) |
| CA (1) | CA3003589C (https=) |
| WO (1) | WO2017075580A1 (https=) |
Families Citing this family (16)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP6342575B2 (ja) * | 2014-08-13 | 2018-06-13 | ザ・ジョンズ・ホプキンス・ユニバーシティー | 脳腫瘍への選択的デンドリマー送達 |
| IL270169B2 (en) | 2017-04-27 | 2024-08-01 | Univ Johns Hopkins | Dendrimer preparations for use in angiography |
| WO2018208707A1 (en) * | 2017-05-08 | 2018-11-15 | Neurovia, Inc. | Methods and compositions for treating demyelinating diseases |
| US11918657B2 (en) | 2017-11-10 | 2024-03-05 | The Johns Hopkins University | Dendrimer delivery system and methods of use thereof |
| WO2019118951A2 (en) * | 2017-12-15 | 2019-06-20 | Duke University | Compositions and methods of enhancing the homing and/or engraftment of hematopoietic cells in the central nervous system |
| WO2020081923A1 (en) * | 2018-10-19 | 2020-04-23 | Disarm Therapeutics, Inc. | Inhibitors of sarm1 in combination with nad+ or a nad+ precursor |
| WO2020142373A1 (en) * | 2019-01-02 | 2020-07-09 | Mayo Foundation For Medical Education And Research | Methods and materials for treating leukodystrophies |
| JP7759322B2 (ja) | 2019-12-04 | 2025-10-23 | アシュバッタ セラピューティクス， インコーポレイテッド | 眼に薬物送達するためのデンドリマー組成物および方法 |
| PH12022552818A1 (en) * | 2020-04-24 | 2024-03-25 | Ashvattha Therapeutics Inc | Dendrimer compositions and methods for treatment of severe acute respiratory distress syndrome |
| US20230364244A1 (en) * | 2020-07-17 | 2023-11-16 | Ashvattha Therapeutics, Inc. | Dendrimer compositions and methods for drug delivery to injured kidney |
| WO2023081750A1 (en) * | 2021-11-04 | 2023-05-11 | The Children's Hospital Of Philadelphia | Compositions and methods for treating metachromatic leukodystrophy disease and related disorders |
| WO2024081687A2 (en) * | 2022-10-12 | 2024-04-18 | The Johns Hopkins University | Method of treating lbsl by enhancing dars2 expression |
| CN116082153A (zh) * | 2022-12-09 | 2023-05-09 | 长沙贝塔医药科技有限公司 | 一种丙烯酸酯类衍生物-13c的制备方法 |
| EP4410284A1 (en) * | 2023-02-02 | 2024-08-07 | Apteeus | Compound and method for the treatment of zellweger spectrum disorder |
| CN117643581A (zh) * | 2023-11-29 | 2024-03-05 | 徐州医科大学 | 白藜芦醇在制备激活sirt1基因的药物中的应用 |
| WO2025240286A1 (en) * | 2024-05-14 | 2025-11-20 | Washington State University | Neuron targeted 2-deoxyglucose dendrimer for imaging and treatment of neurological diseases |
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| DE69612755T2 (de) | 1995-02-07 | 2001-08-23 | Brusilow Enterprises, Llc | Triglyceride und ethylester von phenylalkansäuren und phenylalkensäuren zur behandlung verschiedener erkrankungen |
| AU6269799A (en) * | 1998-09-28 | 2000-04-17 | Johns Hopkins University, The | Adrenoleukodystrophy treatments and drug screening |
| US8148356B2 (en) | 2005-08-24 | 2012-04-03 | Cumberland Pharmaceuticals, Inc. | Acetylcysteine composition and uses therefor |
| MX2008014520A (es) * | 2006-05-22 | 2008-11-27 | Elan Pharm Inc | Preparacion de conjugados polimericos de compuestos terapeuticos, agricolas, y de aditivos para alimentos. |
| PL2214646T3 (pl) * | 2007-10-05 | 2021-12-20 | Wayne State University | Dendrymery do przedłużonego uwalniania związków |
| WO2009134460A1 (en) | 2008-04-29 | 2009-11-05 | Hyperion Therapeutics | Methods of treatment using ammonia-scavenging drugs |
| WO2009142754A1 (en) * | 2008-05-22 | 2009-11-26 | Goverment Of The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Dendritic conjugates and methods of use |
| CA2767163A1 (en) | 2009-06-15 | 2010-12-23 | Wayne State University | Dendrimer based nanodevices for therapeutic and imaging purposes |
| EP2596112A4 (en) | 2010-07-21 | 2015-01-21 | Cumberland Pharmaceuticals Inc | ACETYCYSTEIN COMPOSITIONS AND USE METHOD THEREFOR |
| EP3263102A1 (en) | 2011-09-30 | 2018-01-03 | Horizon Therapeutics, LLC | Methods of therapeutic monitoring of nitrogen scavenging drugs |
| WO2014178892A1 (en) * | 2013-05-03 | 2014-11-06 | Scanlan Thomas S | Use of sobetirome in the treatment of x-linked adrenolenoleukodystrophy |
| US20160122406A1 (en) * | 2013-06-07 | 2016-05-05 | The Administrators Of The Tulane Educational Fund | Analogs of pituitary adenylate cyclase-activating polypeptide (pacap) and methods for their use |
| CN105813690A (zh) | 2013-08-21 | 2016-07-27 | 协和大学 | 树状聚合物-白藜芦醇复合物 |
| CN106659798A (zh) * | 2014-08-13 | 2017-05-10 | 约翰霍普金斯大学 | 树枝状聚合物组合物和在治疗神经与cns病症中的用途 |
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