JP2016503394A - 細胞型へのオリゴヌクレオチド分子の選択的送達のための組成物および方法 - Google Patents
細胞型へのオリゴヌクレオチド分子の選択的送達のための組成物および方法 Download PDFInfo
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Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201261719297P | 2012-10-26 | 2012-10-26 | |
| US61/719,297 | 2012-10-26 | ||
| EP12382413.8 | 2012-10-26 | ||
| EP12382413 | 2012-10-26 | ||
| PCT/EP2013/072411 WO2014064258A1 (en) | 2012-10-26 | 2013-10-25 | Compositions and methods for selective delivery of oligonucleotide molecules to cell types |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2016503394A true JP2016503394A (ja) | 2016-02-04 |
| JP2016503394A5 JP2016503394A5 (https=) | 2016-12-22 |
Family
ID=47148689
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2015538468A Pending JP2016503394A (ja) | 2012-10-26 | 2013-10-25 | 細胞型へのオリゴヌクレオチド分子の選択的送達のための組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (3) | US9938525B2 (https=) |
| EP (1) | EP2911697A1 (https=) |
| JP (1) | JP2016503394A (https=) |
| AU (1) | AU2013336582A1 (https=) |
| CA (1) | CA2889608A1 (https=) |
| MX (1) | MX2015005328A (https=) |
| WO (1) | WO2014064258A1 (https=) |
Cited By (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JPWO2023027125A1 (https=) * | 2021-08-24 | 2023-03-02 |
Families Citing this family (40)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003222568B2 (en) | 2002-01-11 | 2009-05-07 | Bioasis Technologies, Inc. | Use of P97 as an enzyme delivery system for the delivery of therapeutic lysosomal enzymes |
| RU2664452C2 (ru) | 2010-04-19 | 2018-08-17 | Нлифе Терапеутикс, С.Л. | Конъюгат, медицинское средство и способы лечения и/или профилактики депрессии и болезни, связанной с отложением телец Леви |
| WO2012019168A2 (en) | 2010-08-06 | 2012-02-09 | Moderna Therapeutics, Inc. | Engineered nucleic acids and methods of use thereof |
| RU2013120302A (ru) | 2010-10-01 | 2014-11-20 | Модерна Терапьютикс, Инк. | Сконструированные нуклеиновые кислоты и способы их применения |
| EP2691101A2 (en) | 2011-03-31 | 2014-02-05 | Moderna Therapeutics, Inc. | Delivery and formulation of engineered nucleic acids |
| ES2582869T3 (es) | 2011-07-05 | 2016-09-15 | Bioasis Technologies Inc | Conjugados de P97-anticuerpo |
| US9150858B2 (en) | 2011-08-04 | 2015-10-06 | Yeda Research And Development Co. Ltd. | Micro-RNAs and compositions comprising same for the treatment and diagnosis of serotonin-, adrenalin-, noradrenalin-, glutamate-, and corticotropin-releasing hormone- associated medical conditions |
| US9464124B2 (en) | 2011-09-12 | 2016-10-11 | Moderna Therapeutics, Inc. | Engineered nucleic acids and methods of use thereof |
| RU2648950C2 (ru) | 2011-10-03 | 2018-04-02 | Модерна Терапьютикс, Инк. | Модифицированные нуклеозиды, нуклеотиды и нуклеиновые кислоты и их применение |
| CN104114572A (zh) | 2011-12-16 | 2014-10-22 | 现代治疗公司 | 经修饰的核苷、核苷酸和核酸组合物 |
| AU2013243948A1 (en) | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of proteins associated with human disease |
| US9572897B2 (en) | 2012-04-02 | 2017-02-21 | Modernatx, Inc. | Modified polynucleotides for the production of cytoplasmic and cytoskeletal proteins |
| US9254311B2 (en) | 2012-04-02 | 2016-02-09 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of proteins |
| US9283287B2 (en) | 2012-04-02 | 2016-03-15 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of nuclear proteins |
| ES2647082T3 (es) | 2012-07-31 | 2017-12-19 | Bioasis Technologies Inc | Proteínas desfosforiladas de la enfermedad de depósito lisosómico y métodos de uso de las mismas |
| AU2013336581A1 (en) | 2012-10-26 | 2015-06-11 | Nlife Therapeutics, S.L. | Compositions and methods for the treatment of Parkinson disease by the selective delivery of oligonucleotide molecules to specific neuron types |
| WO2014081507A1 (en) | 2012-11-26 | 2014-05-30 | Moderna Therapeutics, Inc. | Terminally modified rna |
| JP6586412B2 (ja) | 2013-03-13 | 2019-10-02 | バイオアシス テクノロジーズ インコーポレイテッド | p97のフラグメントおよびその使用 |
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| EP2911697A1 (en) | 2015-09-02 |
| MX2015005328A (es) | 2015-09-25 |
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