JP2013523776A - パーキンソン病および脳のドーパミン作動性ニューロンのその他の障害を処置する方法 - Google Patents
パーキンソン病および脳のドーパミン作動性ニューロンのその他の障害を処置する方法 Download PDFInfo
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| PCT/US2011/031027 WO2011123842A2 (en) | 2010-04-02 | 2011-04-01 | Methods for treating parkinson's disease and other disorders of dopaminergic neurons of the brain |
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| IL278213B2 (en) | 2018-04-27 | 2026-04-01 | Rocket Pharmaceuticals Ltd | A gene therapy vector encoding an e3 ubiquitin protein ligase (park2) and use thereof in treating or inhibiting the onset of parkinson’s disease (pd) |
| WO2022017630A1 (en) | 2020-07-23 | 2022-01-27 | Ucl Business Ltd | GENE THERAPY VECTOR FOR eEF1A2 AND USES THEREOF |
| AR131771A1 (es) | 2023-02-03 | 2025-04-30 | Janssen Pharmaceutica Nv | Vectores de terapia génica para su uso en la enfermedad de parkinson |
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| US6800281B2 (en) * | 2000-11-09 | 2004-10-05 | Oxford Biomedica (Uk) Limited | Lentiviral-mediated growth factor gene therapy for neurodegenerative diseases |
| CN1897977A (zh) * | 2003-10-20 | 2007-01-17 | Ns基因公司 | 帕金森氏病的体内基因治疗 |
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Cited By (2)
| Publication number | Priority date | Publication date | Assignee | Title |
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| JP2021045166A (ja) * | 2015-07-13 | 2021-03-25 | サンガモ セラピューティクス， インコーポレイテッド | ヌクレアーゼ媒介ゲノム遺伝子操作のための送達方法及び組成物 |
| JP7348160B2 (ja) | 2015-07-13 | 2023-09-20 | サンガモ セラピューティクス， インコーポレイテッド | ヌクレアーゼ媒介ゲノム遺伝子操作のための送達方法及び組成物 |
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| EP2552473A4 (en) | 2013-10-23 |
| US20120082650A1 (en) | 2012-04-05 |
| CN102821781A (zh) | 2012-12-12 |
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| WO2011123842A2 (en) | 2011-10-06 |
| AU2011235890A1 (en) | 2012-09-27 |
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