JP2004535801A5 - - Google Patents

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Publication number
JP2004535801A5
JP2004535801A5 JP2002592469A JP2002592469A JP2004535801A5 JP 2004535801 A5 JP2004535801 A5 JP 2004535801A5 JP 2002592469 A JP2002592469 A JP 2002592469A JP 2002592469 A JP2002592469 A JP 2002592469A JP 2004535801 A5 JP2004535801 A5 JP 2004535801A5
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JP
Japan
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mck
promoter
amplify
upstream
downstream
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JP2002592469A
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English (en)
Japanese (ja)
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JP2004535801A (ja
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Priority claimed from PCT/US2002/016748 external-priority patent/WO2002095006A2/en
Publication of JP2004535801A publication Critical patent/JP2004535801A/ja
Publication of JP2004535801A5 publication Critical patent/JP2004535801A5/ja
Pending legal-status Critical Current

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JP2002592469A 2001-05-24 2002-05-22 筋特異的発現ベクター Pending JP2004535801A (ja)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US29330401P 2001-05-24 2001-05-24
PCT/US2002/016748 WO2002095006A2 (en) 2001-05-24 2002-05-22 Muscle-specific expression vectors

Publications (2)

Publication Number Publication Date
JP2004535801A JP2004535801A (ja) 2004-12-02
JP2004535801A5 true JP2004535801A5 (cg-RX-API-DMAC7.html) 2006-01-05

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ID=23128549

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2002592469A Pending JP2004535801A (ja) 2001-05-24 2002-05-22 筋特異的発現ベクター

Country Status (7)

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US (2) US20030100526A1 (cg-RX-API-DMAC7.html)
EP (2) EP2017338A1 (cg-RX-API-DMAC7.html)
JP (1) JP2004535801A (cg-RX-API-DMAC7.html)
AT (1) ATE428777T1 (cg-RX-API-DMAC7.html)
CA (1) CA2448120A1 (cg-RX-API-DMAC7.html)
DE (1) DE60231975D1 (cg-RX-API-DMAC7.html)
WO (1) WO2002095006A2 (cg-RX-API-DMAC7.html)

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US12319929B2 (en) 2018-05-15 2025-06-03 Voyager Therapeutics, Inc. Compositions and methods for the treatment of Parkinson's disease
US20210230632A1 (en) 2018-05-15 2021-07-29 Voyager Therapeutics, Inc. Compositions and methods for delivery of aav
US12060567B2 (en) 2018-06-13 2024-08-13 Voyager Therapeutics, Inc. Engineered untranslated regions (UTR) for AAV production
CN112567035A (zh) 2018-07-02 2021-03-26 沃雅戈治疗公司 肌萎缩侧索硬化症及脊髓相关病症的治疗
US20210348242A1 (en) 2018-10-04 2021-11-11 Voyager Therapeutics, Inc. Methods for measuring the titer and potency of viral vector particles
US20210348194A1 (en) 2018-10-05 2021-11-11 Voyager Therapeutics, Inc. Engineered nucleic acid constructs encoding aav production proteins
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BR112021009481A2 (pt) 2018-11-16 2021-08-17 Astellas Pharma Inc. método para tratamento da distrofia muscular direcionando gene de utrofina.
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WO2021247995A2 (en) 2020-06-04 2021-12-09 Voyager Therapeutics, Inc. Compositions and methods of treating neuropathic pain
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JP2025503637A (ja) 2022-01-09 2025-02-04 クリヤ セラピューティクス, インコーポレイテッド 治療用抗igf-1r抗体をコードする核酸の送達のためのベクター構築物およびそれを使用する方法
CN118829729A (zh) * 2022-03-16 2024-10-22 罗格斯新泽西州立大学 受控的肌肉特异性基因递送
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AU2001261063A1 (en) * 2000-04-28 2001-11-12 Xiao Xiao Dna sequences encoding dystrophin minigenes and methods of use thereof
WO2001083703A2 (en) * 2000-05-04 2001-11-08 California Institute Of Technology Checkpoint-activating oligonucleotides

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