JP2001517221A5 - - Google Patents

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Publication number
JP2001517221A5
JP2001517221A5 JP1998540610A JP54061098A JP2001517221A5 JP 2001517221 A5 JP2001517221 A5 JP 2001517221A5 JP 1998540610 A JP1998540610 A JP 1998540610A JP 54061098 A JP54061098 A JP 54061098A JP 2001517221 A5 JP2001517221 A5 JP 2001517221A5
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JP
Japan
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP1998540610A
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English (en)
Japanese (ja)
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JP2001517221A (ja
JP4289687B2 (ja
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Publication date
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Priority claimed from PCT/US1998/004790 external-priority patent/WO1998041240A1/en
Publication of JP2001517221A publication Critical patent/JP2001517221A/ja
Publication of JP2001517221A5 publication Critical patent/JP2001517221A5/ja
Application granted granted Critical
Publication of JP4289687B2 publication Critical patent/JP4289687B2/ja
Anticipated expiration legal-status Critical
Expired - Lifetime legal-status Critical Current

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JP54061098A 1997-03-14 1998-03-12 血友病の治療のための遺伝子治療で使用する方法と組成物 Expired - Lifetime JP4289687B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US4071197P 1997-03-14 1997-03-14
US60/040,711 1997-03-14
PCT/US1998/004790 WO1998041240A1 (en) 1997-03-14 1998-03-12 Methods and compositions for use in gene therapy for treatment of hemophilia

Publications (3)

Publication Number Publication Date
JP2001517221A JP2001517221A (ja) 2001-10-02
JP2001517221A5 true JP2001517221A5 (https=) 2005-11-10
JP4289687B2 JP4289687B2 (ja) 2009-07-01

Family

ID=21912503

Family Applications (1)

Application Number Title Priority Date Filing Date
JP54061098A Expired - Lifetime JP4289687B2 (ja) 1997-03-14 1998-03-12 血友病の治療のための遺伝子治療で使用する方法と組成物

Country Status (9)

Country Link
US (3) US6093392A (https=)
EP (1) EP1005376B1 (https=)
JP (1) JP4289687B2 (https=)
AT (1) ATE486614T1 (https=)
AU (1) AU745386B2 (https=)
CA (1) CA2283639A1 (https=)
DE (1) DE69841982D1 (https=)
ES (1) ES2355588T3 (https=)
WO (1) WO1998041240A1 (https=)

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US8927269B2 (en) 2003-05-19 2015-01-06 The United States Of America, As Represented By The Secretary, Department Of Health And Human Services Avian adenoassociated virus and uses thereof
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US8137960B2 (en) 2003-12-04 2012-03-20 The United States Of America As Represented By The Department Of Health And Human Services Bovine adeno-associated viral (BAAV) vector and uses thereof
WO2005077333A2 (en) * 2004-02-10 2005-08-25 University Of Florida Research Foundation, Inc. Gel-based delivery of recombinant adeno-associated virus vectors
US7722596B2 (en) * 2004-02-26 2010-05-25 Osprey Medical, Inc. Regional cardiac tissue treatment
US20060148742A1 (en) * 2004-02-26 2006-07-06 Kaye David M Polynucleotide delivery to cardiac tissue
WO2006036502A2 (en) 2004-09-22 2006-04-06 St. Jude Children's Research Hospital Improved expression of factor ix in gene therapy vectors
JP5136766B2 (ja) 2004-12-15 2013-02-06 ユニバーシティ オブ ノース カロライナ アット チャペル ヒル キメラベクター
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US8152786B2 (en) * 2006-11-07 2012-04-10 Osprey Medical, Inc. Collection catheter and kit
US9050400B2 (en) * 2008-08-12 2015-06-09 Osprey Medical, Inc. Remote sensing catheter system and methods
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WO2010093784A2 (en) 2009-02-11 2010-08-19 The University Of North Carolina At Chapel Hill Modified virus vectors and methods of making and using the same
FR2952374B1 (fr) * 2009-11-06 2012-11-16 Univ Claude Bernard Lyon Production de facteur ix recombinant dans une lignee cellulaire hepatocytaire humaine
WO2011057243A2 (en) * 2009-11-09 2011-05-12 University Of Central Florida Research Foundation, Inc. Administration of plant expressed oral tolerance agents
US9050291B2 (en) * 2009-12-08 2015-06-09 Health Research Inc. Methods and compositions using peroxiredoxin 1 (PRX1) as an adjuvant
US9295816B2 (en) * 2009-12-09 2016-03-29 Osprey Medical, Inc. Catheter with distal and proximal ports
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US9175280B2 (en) 2010-10-12 2015-11-03 Sangamo Biosciences, Inc. Methods and compositions for treating hemophilia B
RU2013154295A (ru) 2011-06-08 2015-07-20 Шир Хьюман Дженетик Терапис, Инк. КОМПОЗИЦИИ ЛИПИДНЫХ НАНОЧАСТИЦ И СПОСОБЫ ДЛЯ ДОСТАВКИ мРНК
US9155784B2 (en) 2011-06-20 2015-10-13 Icahn School Of Medicine At Mount Sinai Anti-TNF-α therapy for the mucopolysaccharidoses and other lysosomal disorders
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ES2934848T3 (es) * 2015-12-11 2023-02-27 Univ Pennsylvania Método de purificación escalable para AAV8
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US10896749B2 (en) 2017-01-27 2021-01-19 Shire Human Genetic Therapies, Inc. Drug monitoring tool
CN110945127B (zh) 2017-05-22 2024-07-12 武田药品工业株式会社 用于血友病b的基因疗法的编码具有增加的表达的重组fix的病毒载体
WO2019083171A2 (ko) 2017-10-26 2019-05-02 주식회사 큐로진생명과학 솔루블 vegfr-1 변이체 cdna를 함유하는 raav를 포함하는 황반변성 치료용 조성물
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US5866552A (en) * 1996-09-06 1999-02-02 The Trustees Of The University Of Pennsylvania Method for expressing a gene in the absence of an immune response
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