JP2001517221A5 - - Google Patents

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Publication number
JP2001517221A5
JP2001517221A5 JP1998540610A JP54061098A JP2001517221A5 JP 2001517221 A5 JP2001517221 A5 JP 2001517221A5 JP 1998540610 A JP1998540610 A JP 1998540610A JP 54061098 A JP54061098 A JP 54061098A JP 2001517221 A5 JP2001517221 A5 JP 2001517221A5
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JP
Japan
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP1998540610A
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English (en)
Japanese (ja)
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JP4289687B2 (ja
JP2001517221A (ja
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Publication date
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Priority claimed from PCT/US1998/004790 external-priority patent/WO1998041240A1/en
Publication of JP2001517221A publication Critical patent/JP2001517221A/ja
Publication of JP2001517221A5 publication Critical patent/JP2001517221A5/ja
Application granted granted Critical
Publication of JP4289687B2 publication Critical patent/JP4289687B2/ja
Anticipated expiration legal-status Critical
Expired - Lifetime legal-status Critical Current

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JP54061098A 1997-03-14 1998-03-12 血友病の治療のための遺伝子治療で使用する方法と組成物 Expired - Lifetime JP4289687B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US4071197P 1997-03-14 1997-03-14
US60/040,711 1997-03-14
PCT/US1998/004790 WO1998041240A1 (en) 1997-03-14 1998-03-12 Methods and compositions for use in gene therapy for treatment of hemophilia

Publications (3)

Publication Number Publication Date
JP2001517221A JP2001517221A (ja) 2001-10-02
JP2001517221A5 true JP2001517221A5 (OSRAM) 2005-11-10
JP4289687B2 JP4289687B2 (ja) 2009-07-01

Family

ID=21912503

Family Applications (1)

Application Number Title Priority Date Filing Date
JP54061098A Expired - Lifetime JP4289687B2 (ja) 1997-03-14 1998-03-12 血友病の治療のための遺伝子治療で使用する方法と組成物

Country Status (9)

Country Link
US (3) US6093392A (OSRAM)
EP (1) EP1005376B1 (OSRAM)
JP (1) JP4289687B2 (OSRAM)
AT (1) ATE486614T1 (OSRAM)
AU (1) AU745386B2 (OSRAM)
CA (1) CA2283639A1 (OSRAM)
DE (1) DE69841982D1 (OSRAM)
ES (1) ES2355588T3 (OSRAM)
WO (1) WO1998041240A1 (OSRAM)

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US20030198620A1 (en) * 2002-04-16 2003-10-23 Keiya Ozawa Method of treating amino acid metabolic disorders using recombinant adeno-associated virus virions
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US8927269B2 (en) 2003-05-19 2015-01-06 The United States Of America, As Represented By The Secretary, Department Of Health And Human Services Avian adenoassociated virus and uses thereof
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WO2005056807A2 (en) 2003-12-04 2005-06-23 The Government Of The United States Of America, As Represented By The Secretary, Department Of Health And Human Services, National Institutes Of Health Bovine adeno-associated viral (baav) vector and uses thereof
US20060078542A1 (en) * 2004-02-10 2006-04-13 Mah Cathryn S Gel-based delivery of recombinant adeno-associated virus vectors
US20060148742A1 (en) * 2004-02-26 2006-07-06 Kaye David M Polynucleotide delivery to cardiac tissue
US7722596B2 (en) * 2004-02-26 2010-05-25 Osprey Medical, Inc. Regional cardiac tissue treatment
DK1804839T3 (da) 2004-09-22 2012-04-10 St Jude Childrens Res Hospital Forbedret ekspression af faktor ix i genterapivektorer
AU2005316476A1 (en) 2004-12-15 2006-06-22 University Of Florida Research Foundation, Inc. Chimeric vectors
US8283151B2 (en) 2005-04-29 2012-10-09 The United States Of America, As Represented By The Secretary, Department Of Health And Human Services Isolation, cloning and characterization of new adeno-associated virus (AAV) serotypes
US8152786B2 (en) * 2006-11-07 2012-04-10 Osprey Medical, Inc. Collection catheter and kit
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US20100041984A1 (en) * 2008-08-12 2010-02-18 James Edward Shapland Impedance sensing device and catheter system
US8889641B2 (en) 2009-02-11 2014-11-18 The University Of North Carolina At Chapel Hill Modified virus vectors and methods of making and using the same
FR2952374B1 (fr) * 2009-11-06 2012-11-16 Univ Claude Bernard Lyon Production de facteur ix recombinant dans une lignee cellulaire hepatocytaire humaine
WO2011057243A2 (en) * 2009-11-09 2011-05-12 University Of Central Florida Research Foundation, Inc. Administration of plant expressed oral tolerance agents
IN2012DN04875A (OSRAM) * 2009-12-08 2015-09-25 Health Research Inc
US9295816B2 (en) * 2009-12-09 2016-03-29 Osprey Medical, Inc. Catheter with distal and proximal ports
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KR101930711B1 (ko) 2010-10-12 2018-12-19 더 칠드런스 호스피탈 오브 필라델피아 혈우병 b의 치료를 위한 방법 및 조성물
PT2717893T (pt) * 2011-06-08 2019-08-20 Translate Bio Inc Composições de nanopartículas lipídicas e métodos para transferência de arnm
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WO2019083171A2 (ko) 2017-10-26 2019-05-02 주식회사 큐로진생명과학 솔루블 vegfr-1 변이체 cdna를 함유하는 raav를 포함하는 황반변성 치료용 조성물
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