ES3007212T3 - Use of migalostat in reducing the risk of cerebrovascular event in patients with fabry disease - Google Patents
Use of migalostat in reducing the risk of cerebrovascular event in patients with fabry disease Download PDFInfo
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- ES3007212T3 ES3007212T3 ES20708283T ES20708283T ES3007212T3 ES 3007212 T3 ES3007212 T3 ES 3007212T3 ES 20708283 T ES20708283 T ES 20708283T ES 20708283 T ES20708283 T ES 20708283T ES 3007212 T3 ES3007212 T3 ES 3007212T3
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- A61K31/00—Medicinal preparations containing organic active ingredients
- A61K31/33—Heterocyclic compounds
- A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
- A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
- A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
- A61K31/445—Non condensed piperidines, e.g. piperocaine
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P25/00—Drugs for disorders of the nervous system
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
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- A—HUMAN NECESSITIES
- A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
- A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
- A61P9/00—Drugs for disorders of the cardiovascular system
- A61P9/10—Drugs for disorders of the cardiovascular system for treating ischaemic or atherosclerotic diseases, e.g. antianginal drugs, coronary vasodilators, drugs for myocardial infarction, retinopathy, cerebrovascula insufficiency, renal arteriosclerosis
Landscapes
- Health & Medical Sciences (AREA)
- Veterinary Medicine (AREA)
- Public Health (AREA)
- General Health & Medical Sciences (AREA)
- Animal Behavior & Ethology (AREA)
- Chemical & Material Sciences (AREA)
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- Engineering & Computer Science (AREA)
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- Organic Chemistry (AREA)
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- Vascular Medicine (AREA)
- Biomedical Technology (AREA)
- Neurology (AREA)
- Neurosurgery (AREA)
- Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
- Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
- Medicines Containing Material From Animals Or Micro-Organisms (AREA)
- Enzymes And Modification Thereof (AREA)
Applications Claiming Priority (2)
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| US201962795524P | 2019-01-22 | 2019-01-22 | |
| PCT/US2020/014531 WO2020154354A1 (en) | 2019-01-22 | 2020-01-22 | Use of migalostat in reducing the risk of cerebrovascular event in patients with fabry disease |
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| ES3007212T3 true ES3007212T3 (en) | 2025-03-19 |
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| US12594268B2 (en) * | 2018-08-20 | 2026-04-07 | Amicus Therapeutics, Inc. | Methods of treating Fabry disease in patients having a mutation in the GLA gene |
| KR20220044560A (ko) | 2019-08-07 | 2022-04-08 | 아미쿠스 세라퓨틱스, 인코포레이티드 | Gla 유전자에 돌연변이를 갖는 환자에서 파브리 질병을 치료하는 방법 |
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| US6274597B1 (en) | 1998-06-01 | 2001-08-14 | Mount Sinai School Of Medicine Of New York University | Method of enhancing lysosomal α-Galactosidase A |
| MX2009010557A (es) | 2007-03-30 | 2009-11-19 | Amicus Therapeutics Inc | Metodo para el tratamiento de la enfermedad de fabry que utiliza chaperonas farmacologicas. |
| US9999618B2 (en) * | 2007-04-26 | 2018-06-19 | Amicus Therapeutics, Inc. | Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones |
| EP2946785B1 (en) | 2008-02-12 | 2018-10-24 | Amicus Therapeutics, Inc. | Method to predict response to pharmacological chaperone treatment of diseases |
| TW202408513A (zh) * | 2016-07-19 | 2024-03-01 | 美商阿米庫斯醫療股份有限公司 | 治療ert初治的和已經歷ert的患者中之法布瑞氏症 |
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Also Published As
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|---|---|
| PT3914247T (pt) | 2025-01-23 |
| PL3914247T3 (pl) | 2025-04-14 |
| EP3914247B1 (en) | 2024-11-13 |
| FI3914247T3 (fi) | 2025-02-16 |
| RS66410B1 (sr) | 2025-02-28 |
| LT3914247T (lt) | 2025-01-27 |
| SI3914247T1 (sl) | 2025-03-31 |
| HRP20250078T1 (hr) | 2025-03-28 |
| DK3914247T3 (da) | 2025-01-27 |
| SMT202500034T1 (it) | 2025-03-12 |
| HUE069934T2 (hu) | 2025-04-28 |
| EP3914247A1 (en) | 2021-12-01 |
| WO2020154354A1 (en) | 2020-07-30 |
| JP2022518733A (ja) | 2022-03-16 |
| EP4523750A3 (en) | 2025-06-11 |
| JP2025128105A (ja) | 2025-09-02 |
| US20220087993A1 (en) | 2022-03-24 |
| TW202042812A (zh) | 2020-12-01 |
| AR117861A1 (es) | 2021-09-01 |
| JP7680356B2 (ja) | 2025-05-20 |
| EP4523750A2 (en) | 2025-03-19 |
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