CN117561067A - 用于治疗h-abc脑白质营养不良的组合物和方法 - Google Patents
用于治疗h-abc脑白质营养不良的组合物和方法 Download PDFInfo
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163175988P | 2021-04-16 | 2021-04-16 | |
| US63/175,988 | 2021-04-16 | ||
| PCT/US2022/025246 WO2022221777A1 (en) | 2021-04-16 | 2022-04-18 | Compositions and methods useful for the treatment of h-abc leukodystrophy |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| CN117561067A true CN117561067A (zh) | 2024-02-13 |
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Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| CN202280043000.2A Pending CN117561067A (zh) | 2021-04-16 | 2022-04-18 | 用于治疗h-abc脑白质营养不良的组合物和方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20240200065A1 (https=) |
| EP (1) | EP4323063A4 (https=) |
| JP (1) | JP2024515289A (https=) |
| CN (1) | CN117561067A (https=) |
| AU (1) | AU2022257101A1 (https=) |
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| WO2020227713A1 (en) * | 2019-05-09 | 2020-11-12 | The Children's Hospital Of Philadelphia | Compositions and methods for the treatment of leukodystrophy and whole animal and cellular models for the identifying efficacious agents for treatment of the same |
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| WO2022221777A1 (en) | 2022-10-20 |
| US20240200065A1 (en) | 2024-06-20 |
| AU2022257101A9 (en) | 2023-11-09 |
| JP2024515289A (ja) | 2024-04-08 |
| CA3215478A1 (en) | 2022-10-20 |
| AU2022257101A1 (en) | 2023-11-02 |
| EP4323063A4 (en) | 2025-05-14 |
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