CN115335062A - 肌肉靶向复合物及其用于调节与肌肉健康相关的基因的用途 - Google Patents

肌肉靶向复合物及其用于调节与肌肉健康相关的基因的用途 Download PDF

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CN115335062A
CN115335062A CN202180018131.0A CN202180018131A CN115335062A CN 115335062 A CN115335062 A CN 115335062A CN 202180018131 A CN202180018131 A CN 202180018131A CN 115335062 A CN115335062 A CN 115335062A
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cdr
amino acid
seq
acid sequence
antibody
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罗梅什·R·苏布拉马尼亚
穆罕默德·T·卡塔纳尼
科迪·A·德雅尔丹
邓肯·布朗
维克托·科特利安斯基
蒂莫西·威登
布伦丹·奎因
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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    • C07K16/2881Immunoglobulins [IG], e.g. monoclonal or polyclonal antibodies against material from animals or humans against receptors, cell surface antigens or cell surface determinants against CD71
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CN202180018131.0A 2020-01-10 2021-01-08 肌肉靶向复合物及其用于调节与肌肉健康相关的基因的用途 Pending CN115335062A (zh)

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US202062959590P 2020-01-10 2020-01-10
US202062959469P 2020-01-10 2020-01-10
US202062959398P 2020-01-10 2020-01-10
US62/959,398 2020-01-10
US62/959,590 2020-01-10
US62/959,469 2020-01-10
PCT/US2021/012650 WO2021142227A1 (en) 2020-01-10 2021-01-08 Muscle targeting complexes and uses thereof for modulation of genes associated with muscle health

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US (1) US20230111147A1 (enExample)
EP (1) EP4087586A4 (enExample)
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CA (1) CA3163283A1 (enExample)
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US11911484B2 (en) 2018-08-02 2024-02-27 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
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JP2024525608A (ja) 2021-07-09 2024-07-12 ダイン セラピューティクス,インコーポレーテッド ジストロフィン異常症を処置するための筋標的化複合体および製剤
US11633498B2 (en) 2021-07-09 2023-04-25 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US11771776B2 (en) 2021-07-09 2023-10-03 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
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US11969475B2 (en) 2021-07-09 2024-04-30 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating facioscapulohumeral muscular dystrophy
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WO2024220863A1 (en) * 2023-04-20 2024-10-24 University Of Massachusetts Rna therapeutics for fibrodysplasia ossificans progressiva and uses thereof
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EP4087586A4 (en) 2024-05-08
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CA3163283A1 (en) 2021-07-15
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