CN113166240A - 肌肉靶向复合物及其用于治疗弗里德赖希共济失调的用途 - Google Patents

肌肉靶向复合物及其用于治疗弗里德赖希共济失调的用途 Download PDF

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CN113166240A
CN113166240A CN201980064588.8A CN201980064588A CN113166240A CN 113166240 A CN113166240 A CN 113166240A CN 201980064588 A CN201980064588 A CN 201980064588A CN 113166240 A CN113166240 A CN 113166240A
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complex
antibody
muscle
transferrin receptor
oligonucleotide
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罗梅什·R·苏布拉马尼亚
穆罕默德·T·卡塔纳尼
蒂莫西·威登
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Dyne Therapeutics Inc
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Dyne Therapeutics Inc
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CN201980064588.8A 2018-08-02 2019-08-02 肌肉靶向复合物及其用于治疗弗里德赖希共济失调的用途 Pending CN113166240A (zh)

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US201862714035P 2018-08-02 2018-08-02
US62/714,035 2018-08-02
PCT/US2019/044959 WO2020028840A1 (en) 2018-08-02 2019-08-02 Muscle targeting complexes and uses thereof for treating friedreich's ataxia

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CN (1) CN113166240A (enExample)
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EA (1) EA202190419A1 (enExample)
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US11911484B2 (en) 2018-08-02 2024-02-27 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
US11168141B2 (en) 2018-08-02 2021-11-09 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
EA202190416A1 (ru) 2018-08-02 2021-06-23 Дайн Терапьютикс, Инк. Мышечно-специфические комлексы и их применение для лечения плече-лопаточно-лицевой мышечной дистрофии
US12097263B2 (en) 2018-08-02 2024-09-24 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating myotonic dystrophy
MX2021001281A (es) 2018-08-02 2021-07-15 Dyne Therapeutics Inc Complejos dirigidos a músculos y sus usos para el tratamiento de distrofinopatías.
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