CN111440796A - 用于治疗肌营养不良症的改良的外显子跳跃组合物 - Google Patents

用于治疗肌营养不良症的改良的外显子跳跃组合物 Download PDF

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CN111440796A
CN111440796A CN202010276936.2A CN202010276936A CN111440796A CN 111440796 A CN111440796 A CN 111440796A CN 202010276936 A CN202010276936 A CN 202010276936A CN 111440796 A CN111440796 A CN 111440796A
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oligonucleotide
antisense
exon
dystrophin
substituted
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Chinese (zh)
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理查德·K·贝斯特威克
黛安·伊丽莎白·弗兰克
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Sarepta Therapeutics Inc
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Sarepta Therapeutics Inc
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CN202010276936.2A 2012-12-20 2013-12-20 用于治疗肌营养不良症的改良的外显子跳跃组合物 Pending CN111440796A (zh)

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US201261739968P 2012-12-20 2012-12-20
US61/739,968 2012-12-20
CN201380073536.XA CN106414739A (zh) 2012-12-20 2013-12-20 用于治疗肌营养不良症的改良的外显子跳跃组合物

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CN201380073536.XA Pending CN106414739A (zh) 2012-12-20 2013-12-20 用于治疗肌营养不良症的改良的外显子跳跃组合物

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US (5) US20150361428A1 (https=)
EP (2) EP3885439A1 (https=)
JP (3) JP2016502858A (https=)
KR (2) KR20150099804A (https=)
CN (2) CN111440796A (https=)
AU (3) AU2013364158A1 (https=)
BR (1) BR112015014987A2 (https=)
CA (1) CA2894899A1 (https=)
EA (1) EA201591178A1 (https=)
HK (1) HK1216902A1 (https=)
IL (1) IL239491A0 (https=)
MX (2) MX2015008035A (https=)
WO (1) WO2014100714A1 (https=)

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