CA3001574A1 - Codon-optimized reduced-size atp7a cdna and uses for treatment of copper transport disorders - Google Patents
Codon-optimized reduced-size atp7a cdna and uses for treatment of copper transport disorders Download PDFInfo
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- CA3001574A1 CA3001574A1 CA3001574A CA3001574A CA3001574A1 CA 3001574 A1 CA3001574 A1 CA 3001574A1 CA 3001574 A CA3001574 A CA 3001574A CA 3001574 A CA3001574 A CA 3001574A CA 3001574 A1 CA3001574 A1 CA 3001574A1
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- copper
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
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| US201562244594P | 2015-10-21 | 2015-10-21 | |
| US62/244,594 | 2015-10-21 | ||
| PCT/US2016/058124 WO2017070472A1 (en) | 2015-10-21 | 2016-10-21 | Codon-optimized reduced-size atp7a cdna and uses for treatment of copper transport disorders |
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| CA3001574A1 true CA3001574A1 (en) | 2017-04-27 |
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| CA3001574A Pending CA3001574A1 (en) | 2015-10-21 | 2016-10-21 | Codon-optimized reduced-size atp7a cdna and uses for treatment of copper transport disorders |
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| WO2020014594A1 (en) * | 2018-07-12 | 2020-01-16 | The Taxas A&M University System | Compositions for the treatment of copper deficiency and methods of use |
| AU2022240726A1 (en) * | 2021-03-18 | 2023-09-21 | Cyprium Therapeutics, Inc. | Copper histidinate compositions and uses thereof |
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| WO1993017321A1 (en) | 1992-02-25 | 1993-09-02 | Unisearch Limited | Electrothermal atomic absorption and preconcentration device |
| DE606516T1 (de) | 1993-01-13 | 1995-03-16 | Idemitsu Kosan Co | Gegen menschlichen Ceruloplasmin monoklonaler Antikörper. |
| US6759050B1 (en) | 1998-12-03 | 2004-07-06 | Avigen, Inc. | Excipients for use in adeno-associated virus pharmaceutical formulations, and pharmaceutical formulations made therewith |
| US6812339B1 (en) * | 2000-09-08 | 2004-11-02 | Applera Corporation | Polymorphisms in known genes associated with human disease, methods of detection and uses thereof |
| KR100459644B1 (ko) | 2001-03-31 | 2004-12-03 | 제노백(주) | 혈액 여과지에서의 효소면역측정법을 이용한셀룰로플라스민 농도 측정 방법 및 이 방법을 이용한윌슨병 스크리닝 검사용 키트와 진단 시약 |
| EP1625210B1 (en) | 2003-05-21 | 2010-12-01 | Genzyme Corporation | Methods for producing preparations of recombinant aav virions substantially free of empty capsids |
| US20070161120A1 (en) | 2006-01-10 | 2007-07-12 | Viorica Lopez-Avila | Ceruloplasmin Assay |
| MX2008012485A (es) * | 2006-03-30 | 2008-10-10 | Novartis Ag | Composiciones y metodos de uso para anticuerpos de c-met. |
| EP2058401A1 (en) * | 2007-10-05 | 2009-05-13 | Genethon | Widespread gene delivery to motor neurons using peripheral injection of AAV vectors |
| WO2009097129A1 (en) | 2008-01-29 | 2009-08-06 | Applied Genetic Technologies Corporation | Recombinant virus production using mammalian cells in suspension |
| WO2010042102A1 (en) | 2008-10-06 | 2010-04-15 | The Government Of The United States Of America As Represented By The Secretary Of The Department Of Health And Human Services | Identification of subjects likely to benefit from copper treatment |
| WO2010071832A1 (en) * | 2008-12-19 | 2010-06-24 | Nationwide Children's Hospital | Delivery of polynucleotides across the blood brain barrier using recombinant aav9 |
| US9415121B2 (en) | 2008-12-19 | 2016-08-16 | Nationwide Children's Hospital | Delivery of MECP2 polynucleotide using recombinant AAV9 |
| US8679837B2 (en) | 2009-04-02 | 2014-03-25 | University Of Florida Research Foundation, Inc. | Inducible system for highly efficient production of recombinant Adeno-associated virus (rAAV) vectors |
| JP6373763B2 (ja) * | 2012-02-17 | 2018-08-22 | ザ・チルドレンズ・ホスピタル・オブ・フィラデルフィアＴｈｅ Ｃｈｉｌｄｒｅｎ’Ｓ Ｈｏｓｐｉｔａｌ Ｏｆ Ｐｈｉｌａｄｅｌｐｈｉａ | Ａａｖベクター成分、及び、細胞、臓器並びに組織への遺伝子導入のための方法 |
| AU2013243949A1 (en) * | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of biologics and proteins associated with human disease |
| AU2013243954A1 (en) | 2012-04-02 | 2014-10-30 | Moderna Therapeutics, Inc. | Modified polynucleotides for the production of cosmetic proteins and peptides |
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| JP6854286B2 (ja) | 2021-04-07 |
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| WO2017070472A1 (en) | 2017-04-27 |
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| AU2016341983B2 (en) | 2022-05-26 |
| US20250129382A1 (en) | 2025-04-24 |
| JP2021052796A (ja) | 2021-04-08 |
| HUE054802T2 (hu) | 2021-09-28 |
| JP2018533941A (ja) | 2018-11-22 |
| US10988778B2 (en) | 2021-04-27 |
| US20180312871A1 (en) | 2018-11-01 |
| AU2016341983A8 (en) | 2022-10-06 |
| US20210214751A1 (en) | 2021-07-15 |
| EP3365438A1 (en) | 2018-08-29 |
| AU2016341983A1 (en) | 2018-04-26 |
| PT3365438T (pt) | 2021-07-12 |
| US12173306B2 (en) | 2024-12-24 |
| CN108431216B (zh) | 2022-08-05 |
| PL3365438T3 (pl) | 2021-10-18 |
| AU2016341983B8 (en) | 2022-10-06 |
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